Detalhe da pesquisa
1.
DNA Deamination Is Required for Human APOBEC3A-Driven Hepatocellular Carcinoma In Vivo.
Int J Mol Sci
; 24(11)2023 May 26.
Artigo
Inglês
| MEDLINE | ID: mdl-37298259
2.
A Preclinical Safety Study of Thyroid Hormone Instilled into the Lungs of Healthy Rats-an Investigational Therapy for ARDS.
J Pharmacol Exp Ther
; 376(1): 74-83, 2021 01.
Artigo
Inglês
| MEDLINE | ID: mdl-33127750
3.
ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome.
Mol Ther
; 27(1): 178-187, 2019 01 02.
Artigo
Inglês
| MEDLINE | ID: mdl-30528089
4.
High-dose enzyme replacement therapy in murine Hurler syndrome.
Mol Genet Metab
; 111(2): 116-22, 2014 Feb.
Artigo
Inglês
| MEDLINE | ID: mdl-24100243
5.
Examination of a blood-brain barrier targeting ß-galactosidase-monoclonal antibody fusion protein in a murine model of GM1-gangliosidosis.
Mol Genet Metab Rep
; 27: 100748, 2021 Jun.
Artigo
Inglês
| MEDLINE | ID: mdl-33854948
6.
Elements of lentiviral vector design toward gene therapy for treating mucopolysaccharidosis I.
Mol Genet Metab Rep
; 8: 87-93, 2016 Sep.
Artigo
Inglês
| MEDLINE | ID: mdl-27556013
7.
Correction of metabolic, craniofacial, and neurologic abnormalities in MPS I mice treated at birth with adeno-associated virus vector transducing the human alpha-L-iduronidase gene.
Mol Ther
; 9(6): 866-75, 2004 Jun.
Artigo
Inglês
| MEDLINE | ID: mdl-15194053