Detalhe da pesquisa
1.
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
N Engl J Med
; 384(21): 2002-2013, 2021 05 27.
Artigo
Inglês
| MEDLINE | ID: mdl-33974366
2.
BCR-JAK2 drives a myeloproliferative neoplasm in transplanted mice.
J Pathol
; 236(2): 219-28, 2015 Jun.
Artigo
Inglês
| MEDLINE | ID: mdl-25664618
3.
Brief report: reduced expression of CD18 leads to the in vivo expansion of hematopoietic stem cells in mouse bone marrow.
Stem Cells
; 32(10): 2794-8, 2014 Oct.
Artigo
Inglês
| MEDLINE | ID: mdl-24906078
4.
Preclinical Optimization and Safety Studies of a New Lentiviral Gene Therapy for p47phox-Deficient Chronic Granulomatous Disease.
Hum Gene Ther
; 32(17-18): 949-958, 2021 09.
Artigo
Inglês
| MEDLINE | ID: mdl-33740872
5.
The downregulated membrane expression of CD18 in CD34+ cells defines a primitive population of human hematopoietic stem cells.
Stem Cell Res Ther
; 11(1): 164, 2020 04 28.
Artigo
Inglês
| MEDLINE | ID: mdl-32345365
6.
Targeted gene correction of human hematopoietic stem cells for the treatment of Wiskott - Aldrich Syndrome.
Nat Commun
; 11(1): 4034, 2020 08 12.
Artigo
Inglês
| MEDLINE | ID: mdl-32788576
7.
Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease.
Mol Ther Methods Clin Dev
; 18: 558-570, 2020 Sep 11.
Artigo
Inglês
| MEDLINE | ID: mdl-32775491
8.
Lentiviral gene therapy for X-linked chronic granulomatous disease.
Nat Med
; 26(2): 200-206, 2020 02.
Artigo
Inglês
| MEDLINE | ID: mdl-31988463
9.
Enhancing Lentiviral and Alpharetroviral Transduction of Human Hematopoietic Stem Cells for Clinical Application.
Mol Ther Methods Clin Dev
; 14: 134-147, 2019 Sep 13.
Artigo
Inglês
| MEDLINE | ID: mdl-31338385
10.
Lentiviral Vector-Mediated Correction of a Mouse Model of Leukocyte Adhesion Deficiency Type I.
Hum Gene Ther
; 27(9): 668-78, 2016 09.
Artigo
Inglês
| MEDLINE | ID: mdl-27056660