Detalhe da pesquisa
1.
Harnessing gene expression to identify the genetic basis of drug resistance.
Mol Syst Biol
; 5: 310, 2009.
Artigo
Inglês
| MEDLINE | ID: mdl-19888205
2.
Slowing late infantile Batten disease by direct brain parenchymal administration of a rh.10 adeno-associated virus expressing CLN2.
Sci Transl Med
; 12(572)2020 12 02.
Artigo
Inglês
| MEDLINE | ID: mdl-33268510
3.
Phase I/II study of intrapleural administration of a serotype rh.10 replication-deficient adeno-associated virus gene transfer vector expressing the human α1-antitrypsin cDNA to individuals with α1-antitrypsin deficiency.
Hum Gene Ther Clin Dev
; 25(3): 112-33, 2014 Sep.
Artigo
Inglês
| MEDLINE | ID: mdl-25238276