Detalhe da pesquisa
1.
Development of a cGMP-compliant process to manufacture donor-derived, CD45RA-depleted memory CD19-CAR T cells.
Gene Ther
; 30(3-4): 222-231, 2023 04.
Artigo
Inglês
| MEDLINE | ID: mdl-34997202
2.
The cost-effectiveness of gene therapy for severe hemophilia B: a microsimulation study from the United States perspective.
Blood
; 138(18): 1677-1690, 2021 11 04.
Artigo
Inglês
| MEDLINE | ID: mdl-33895800
3.
Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1.
N Engl J Med
; 380(16): 1525-1534, 2019 04 18.
Artigo
Inglês
| MEDLINE | ID: mdl-30995372
4.
Sample Stacking Provides Three Orders of Magnitude Sensitivity Enhancement in SDS Capillary Gel Electrophoresis of Adeno-Associated Virus Capsid Proteins.
Anal Chem
; 89(6): 3285-3292, 2017 03 21.
Artigo
Inglês
| MEDLINE | ID: mdl-28277648
5.
A scalable low-cost cGMP process for clinical grade production of the HIV inhibitor 5P12-RANTES in Pichia pastoris.
Protein Expr Purif
; 119: 1-10, 2016 Mar.
Artigo
Inglês
| MEDLINE | ID: mdl-26506568
6.
Integrome signatures of lentiviral gene therapy for SCID-X1 patients.
Sci Adv
; 9(40): eadg9959, 2023 10 06.
Artigo
Inglês
| MEDLINE | ID: mdl-37801507
7.
Common Trajectories of Highly Effective CD19-Specific CAR T Cells Identified by Endogenous T-cell Receptor Lineages.
Cancer Discov
; 12(9): 2098-2119, 2022 09 02.
Artigo
Inglês
| MEDLINE | ID: mdl-35792801
8.
Preferential expansion of CD8+ CD19-CAR T cells postinfusion and the role of disease burden on outcome in pediatric B-ALL.
Blood Adv
; 6(21): 5737-5749, 2022 11 08.
Artigo
Inglês
| MEDLINE | ID: mdl-35446934
9.
Isolation of Pichia pastoris PIR genes and their utilization for cell surface display and recombinant protein secretion.
Yeast
; 28(3): 213-26, 2011 Mar.
Artigo
Inglês
| MEDLINE | ID: mdl-21360733
10.
Purification of a recombinant heavy chain fragment C vaccine candidate against botulinum serotype C neurotoxin [rBoNTC(H(c))] expressed in Pichia pastoris.
Protein Expr Purif
; 75(2): 177-85, 2011 Feb.
Artigo
Inglês
| MEDLINE | ID: mdl-20933089
11.
CD19-CAR T cells undergo exhaustion DNA methylation programming in patients with acute lymphoblastic leukemia.
Cell Rep
; 37(9): 110079, 2021 11 30.
Artigo
Inglês
| MEDLINE | ID: mdl-34852226
12.
Safety and immunogenicity of an intranasal sendai virus-based vaccine for human parainfluenza virus type I and respiratory syncytial virus (SeVRSV) in adults.
Hum Vaccin Immunother
; 17(2): 554-559, 2021 02 01.
Artigo
Inglês
| MEDLINE | ID: mdl-32750273
13.
Fed-batch fermentation of GM-CSF-producing glycoengineered Pichia pastoris under controlled specific growth rate.
Microb Cell Fact
; 9: 93, 2010 Nov 23.
Artigo
Inglês
| MEDLINE | ID: mdl-21092289
14.
Development and Optimization of a Hydrophobic Interaction Chromatography-Based Method of AAV Harvest, Capture, and Recovery.
Mol Ther Methods Clin Dev
; 19: 275-284, 2020 Dec 11.
Artigo
Inglês
| MEDLINE | ID: mdl-33102619
15.
Lentiviral Vector Production from a Stable Packaging Cell Line Using a Packed Bed Bioreactor.
Mol Ther Methods Clin Dev
; 19: 1-13, 2020 Dec 11.
Artigo
Inglês
| MEDLINE | ID: mdl-32995355
16.
A Phase 1 and pharmacokinetic study evaluating daily or weekly schedules of the humanized anti-GD2 antibody hu14.18K322A in recurrent/refractory solid tumors.
MAbs
; 12(1): 1773751, 2020.
Artigo
Inglês
| MEDLINE | ID: mdl-32643524
17.
Highly Sensitive SDS Capillary Gel Electrophoresis with Sample Stacking Requiring Only Nanograms of Adeno-Associated Virus Capsid Proteins.
Methods Mol Biol
; 1972: 263-270, 2019.
Artigo
Inglês
| MEDLINE | ID: mdl-30847798
18.
Cell bank characterization and fermentation optimization for production of recombinant heavy chain C-terminal fragment of botulinum neurotoxin serotype E (rBoNTE(H(c)): antigen E) by Pichia pastoris.
J Biotechnol
; 127(3): 462-74, 2007 Jan 10.
Artigo
Inglês
| MEDLINE | ID: mdl-17010465
19.
Rational design and optimization of fed-batch and continuous fermentations.
Methods Mol Biol
; 389: 43-64, 2007.
Artigo
Inglês
| MEDLINE | ID: mdl-17951634
20.
Saturation of the secretory pathway by overexpression of a hookworm (Necator americanus) Protein (Na-ASP1).
Methods Mol Biol
; 389: 65-76, 2007.
Artigo
Inglês
| MEDLINE | ID: mdl-17951635