Detalhe da pesquisa
1.
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
N Engl J Med
; 384(21): 2002-2013, 2021 05 27.
Artigo
Inglês
| MEDLINE | ID: mdl-33974366
2.
Preclinical studies for a phase 1 clinical trial of autologous hematopoietic stem cell gene therapy for sickle cell disease.
Cytotherapy
; 19(9): 1096-1112, 2017 09.
Artigo
Inglês
| MEDLINE | ID: mdl-28733131
3.
A toxicology study of Csf2ra complementation and pulmonary macrophage transplantation therapy of hereditary PAP in mice.
Mol Ther Methods Clin Dev
; 32(2): 101213, 2024 Jun 13.
Artigo
Inglês
| MEDLINE | ID: mdl-38596536
4.
Defective homing is associated with altered Cdc42 activity in cells from patients with Fanconi anemia group A.
Blood
; 112(5): 1683-6, 2008 Sep 01.
Artigo
Inglês
| MEDLINE | ID: mdl-18565850
5.
The Access Technology Program of the Indiana Clinical Translational Sciences Institute (CTSI): A model to facilitate access to cutting-edge technologies across a state.
J Clin Transl Sci
; 5(1): e33, 2020 Aug 19.
Artigo
Inglês
| MEDLINE | ID: mdl-33948256
6.
Release testing of retroviral vectors and gene-modified cells.
Methods Mol Biol
; 506: 265-79, 2009.
Artigo
Inglês
| MEDLINE | ID: mdl-19110632
7.
Database setup for preclinical studies of gene-modified hematopoiesis.
Methods Mol Biol
; 506: 467-76, 2009.
Artigo
Inglês
| MEDLINE | ID: mdl-19110645
8.
Copy number determination of genetically-modified hematopoietic stem cells.
Methods Mol Biol
; 506: 281-98, 2009.
Artigo
Inglês
| MEDLINE | ID: mdl-19110633
9.
A Scalable Lentiviral Vector Production and Purification Method Using Mustang Q Chromatography and Tangential Flow Filtration.
Methods Mol Biol
; 1937: 135-153, 2019.
Artigo
Inglês
| MEDLINE | ID: mdl-30706394
10.
Production of retroviral vectors for clinical use.
Methods Mol Biol
; 433: 17-32, 2008.
Artigo
Inglês
| MEDLINE | ID: mdl-18679615
11.
Stem cell collection and gene transfer in Fanconi anemia.
Mol Ther
; 15(1): 211-9, 2007 Jan.
Artigo
Inglês
| MEDLINE | ID: mdl-17164793
12.
Lentiviral vectors pseudotyped with murine ecotropic envelope: increased biosafety and convenience in preclinical research.
Exp Hematol
; 34(5): 588-92, 2006 May.
Artigo
Inglês
| MEDLINE | ID: mdl-16647564
13.
Detection of ecotropic replication-competent retroviruses: comparison of s(+)/l(-) and marker rescue assays.
Hum Gene Ther
; 13(14): 1783-90, 2002 Sep 20.
Artigo
Inglês
| MEDLINE | ID: mdl-12396630
14.
Partnership between CTSI and business schools can promote best practices for core facilities and resources.
Clin Transl Sci
; 6(4): 297-302, 2013 Aug.
Artigo
Inglês
| MEDLINE | ID: mdl-23919365
15.
Vector production in an academic environment: a tool to assess production costs.
Hum Gene Ther Methods
; 24(1): 49-57, 2013 Feb.
Artigo
Inglês
| MEDLINE | ID: mdl-23360377
16.
Importance of murine study design for testing toxicity of retroviral vectors in support of phase I trials.
Mol Ther
; 15(4): 782-91, 2007 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-17299409