Detalhe da pesquisa
1.
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3.
Hum Mol Genet
; 31(4): 499-509, 2022 02 21.
Artigo
Inglês
| MEDLINE | ID: mdl-34505136
2.
Modeling Sarcoglycanopathy in Danio rerio.
Int J Mol Sci
; 24(16)2023 Aug 11.
Artigo
Inglês
| MEDLINE | ID: mdl-37628888
3.
Reciprocal Homer1a and Homer2 Isoform Expression Is a Key Mechanism for Muscle Soleus Atrophy in Spaceflown Mice.
Int J Mol Sci
; 23(1)2021 Dec 22.
Artigo
Inglês
| MEDLINE | ID: mdl-35008503
4.
Combined Use of CFTR Correctors in LGMD2D Myotubes Improves Sarcoglycan Complex Recovery.
Int J Mol Sci
; 21(5)2020 Mar 06.
Artigo
Inglês
| MEDLINE | ID: mdl-32155735
5.
Advanced therapeutic approaches in sarcoglycanopathies.
Curr Opin Pharmacol
; 76: 102459, 2024 May 06.
Artigo
Inglês
| MEDLINE | ID: mdl-38713975
6.
Synthesis and Evaluation of Bithiazole Derivatives As Potential α-Sarcoglycan Correctors.
ACS Med Chem Lett
; 14(8): 1049-1053, 2023 Aug 10.
Artigo
Inglês
| MEDLINE | ID: mdl-37583821