Detalhe da pesquisa
1.
BRAF Signaling Pathway Inhibition, Podocyte Injury, and Nephrotic Syndrome.
Am J Kidney Dis
; 70(1): 145-150, 2017 Jul.
Artigo
Inglês
| MEDLINE | ID: mdl-28242136
2.
Orphan drugs - Authors' reply.
Lancet
; 393(10181): 1595-1596, 2019 04 20.
Artigo
Inglês
| MEDLINE | ID: mdl-31007199
3.
Eliminating treatable deaths due to acute kidney injury in resource-poor settings.
Semin Dial
; 28(2): 193-7, 2015.
Artigo
Inglês
| MEDLINE | ID: mdl-25441104
4.
Dramatic effects of eculizumab in a child with diffuse proliferative lupus nephritis resistant to conventional therapy.
Pediatr Nephrol
; 30(1): 167-72, 2015 Jan.
Artigo
Inglês
| MEDLINE | ID: mdl-25173358
5.
Outrageous prices of orphan drugs: a call for collaboration.
Lancet
; 392(10149): 791-794, 2018 09 01.
Artigo
Inglês
| MEDLINE | ID: mdl-30037734
6.
Kidney failure: aims for the next 10 years and barriers to success.
Lancet
; 382(9889): 353-62, 2013 Jul 27.
Artigo
Inglês
| MEDLINE | ID: mdl-23727164
7.
Immunosuppressive treatment for idiopathic membranous nephropathy in adults with nephrotic syndrome.
Cochrane Database Syst Rev
; (10): CD004293, 2014 Oct 16.
Artigo
Inglês
| MEDLINE | ID: mdl-25318831
8.
Rare diseases and effective treatments: are we delivering?
Lancet
; 385(9970): 750-2, 2015 Feb 28.
Artigo
Inglês
| MEDLINE | ID: mdl-25752159
9.
Rare autoimmune diseases.
Adv Exp Med Biol
; 686: 365-74, 2010.
Artigo
Inglês
| MEDLINE | ID: mdl-20824456
10.
Low mortality and key aspects of delivery of care for end-stage renal disease in Italy.
ScientificWorldJournal
; 9: 349-59, 2009 May 21.
Artigo
Inglês
| MEDLINE | ID: mdl-19468656
11.
[Drugs for rare diseases: the blessing of being orphans.] / I farmaci per le malattie rare: la fortuna di essere orfani.
Recenti Prog Med
; 110(5): 221-229, 2019 05.
Artigo
Italiano
| MEDLINE | ID: mdl-31140454
12.
Social/economic costs and health-related quality of life in patients with histiocytosis in Europe.
Eur J Health Econ
; 17 Suppl 1: 67-78, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27042831
13.
Social/economic costs and health-related quality of life in patients with cystic fibrosis in Europe.
Eur J Health Econ
; 17 Suppl 1: 7-18, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27059622
14.
Social/economic costs and quality of life in patients with haemophilia in Europe.
Eur J Health Econ
; 17 Suppl 1: 53-65, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27048374
15.
Social/economic costs and health-related quality of life in patients with fragile X syndrome in Europe.
Eur J Health Econ
; 17 Suppl 1: 43-52, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27072054
16.
Social/economic costs and health-related quality of life of mucopolysaccharidosis patients and their caregivers in Europe.
Eur J Health Econ
; 17 Suppl 1: 89-98, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27062257
17.
Social/economic costs and health-related quality of life in patients with epidermolysis bullosa in Europe.
Eur J Health Econ
; 17 Suppl 1: 31-42, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27107597
18.
Social/economic costs and health-related quality of life in patients with Duchenne muscular dystrophy in Europe.
Eur J Health Econ
; 17 Suppl 1: 19-29, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27038625
19.
Social/economic costs and health-related quality of life in patients with scleroderma in Europe.
Eur J Health Econ
; 17 Suppl 1: 109-17, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27038626
20.
Social/economic costs and health-related quality of life in patients with Prader-Willi syndrome in Europe.
Eur J Health Econ
; 17 Suppl 1: 99-108, 2016 Apr.
Artigo
Inglês
| MEDLINE | ID: mdl-27038627