Detalhe da pesquisa
1.
Adeno-associated virus serotype 2 capsid variants for improved liver-directed gene therapy.
Hepatology
; 77(3): 802-815, 2023 03 01.
Artigo
Inglês
| MEDLINE | ID: mdl-35976053
2.
Small volume bone marrow aspirates with high progenitor cell concentrations maximize cell therapy dose manufacture and substantially reduce donor hemoglobin loss.
BMC Med
; 21(1): 360, 2023 09 19.
Artigo
Inglês
| MEDLINE | ID: mdl-37726769
3.
Gene therapy with adeno-associated virus vector 5-human factor IX in adults with hemophilia B.
Blood
; 131(9): 1022-1031, 2018 03 01.
Artigo
Inglês
| MEDLINE | ID: mdl-29246900
4.
Hyperinflammation in patients with chronic granulomatous disease leads to impairment of hematopoietic stem cell functions.
J Allergy Clin Immunol
; 138(1): 219-228.e9, 2016 07.
Artigo
Inglês
| MEDLINE | ID: mdl-26853280
5.
CD133-targeted gene transfer into long-term repopulating hematopoietic stem cells.
Mol Ther
; 23(1): 63-70, 2015 Jan.
Artigo
Inglês
| MEDLINE | ID: mdl-25189742
6.
Alpharetroviral vector-mediated gene therapy for X-CGD: functional correction and lack of aberrant splicing.
Mol Ther
; 21(3): 648-61, 2013 Mar.
Artigo
Inglês
| MEDLINE | ID: mdl-23207695
7.
Gene therapy of chronic granulomatous disease: the engraftment dilemma.
Mol Ther
; 19(1): 28-35, 2011 Jan.
Artigo
Inglês
| MEDLINE | ID: mdl-21045810
8.
One-year follow-up of the CAPSID randomized trial for high-dose convalescent plasma in severe COVID-19 patients.
J Clin Invest
; 132(24)2022 12 15.
Artigo
Inglês
| MEDLINE | ID: mdl-36326824
9.
First Human Leucocyte Antigen (HLA) Response and Safety Evaluation of Fibrous Demineralized Bone Matrix in a Critical Size Femoral Defect Model of the Sprague-Dawley Rat.
Materials (Basel)
; 13(14)2020 Jul 13.
Artigo
Inglês
| MEDLINE | ID: mdl-32668732
10.
Treatment Options in Hemophilia.
Dtsch Arztebl Int
; 116(47): 791-798, 2019 11 22.
Artigo
Inglês
| MEDLINE | ID: mdl-31847949
11.
High Efficiency Gene Correction in Hematopoietic Cells by Donor-Template-Free CRISPR/Cas9 Genome Editing.
Mol Ther Nucleic Acids
; 10: 1-8, 2018 Mar 02.
Artigo
Inglês
| MEDLINE | ID: mdl-29499925
12.
Wnt signaling regulates transendothelial migration of monocytes.
J Leukoc Biol
; 79(6): 1306-13, 2006 Jun.
Artigo
Inglês
| MEDLINE | ID: mdl-16565323
13.
Constitutive activation of Akt by Flt3 internal tandem duplications is necessary for increased survival, proliferation, and myeloid transformation.
Cancer Res
; 65(21): 9643-50, 2005 Nov 01.
Artigo
Inglês
| MEDLINE | ID: mdl-16266983
14.
Identification of metastasis-associated receptor tyrosine kinases in non-small cell lung cancer.
Cancer Res
; 65(5): 1778-82, 2005 Mar 01.
Artigo
Inglês
| MEDLINE | ID: mdl-15753374
15.
Growth inhibition and induction of apoptosis in acute myeloid leukemia cells by new indolinone derivatives targeting fibroblast growth factor, platelet-derived growth factor, and vascular endothelial growth factor receptors.
Mol Cancer Ther
; 5(12): 3105-12, 2006 Dec.
Artigo
Inglês
| MEDLINE | ID: mdl-17172413
16.
[Gene therapy for septic granulomatosis: risks and opportunities. The road to successful treatment of congenital immunodeficiency]. / Gentherapie der septischen Granulomatose: Chancen und Risiken. Der Weg zur erfolgreichen Therapie einer angeborenen Immundefizienz.
Pharm Unserer Zeit
; 40(3): 264-71, 2011 May.
Artigo
Alemão
| MEDLINE | ID: mdl-21698616
17.
The serine-threonine kinase MNK1 is post-translationally stabilized by PML-RARalpha and regulates differentiation of hematopoietic cells.
Oncogene
; 23(57): 9162-72, 2004 Dec 09.
Artigo
Inglês
| MEDLINE | ID: mdl-15516979
18.
The molecular pathogenesis of acute myeloid leukemia.
Crit Rev Oncol Hematol
; 56(2): 195-221, 2005 Nov.
Artigo
Inglês
| MEDLINE | ID: mdl-16236521
19.
High-throughput analysis of genome-wide receptor tyrosine kinase expression in human cancers identifies potential novel drug targets.
Clin Cancer Res
; 10(4): 1241-9, 2004 Feb 15.
Artigo
Inglês
| MEDLINE | ID: mdl-14977821
20.
Successful Combination of Sequential Gene Therapy and Rescue Allo-HSCT in Two Children with X-CGD - Importance of Timing.
Curr Gene Ther
; 15(4): 416-27, 2015.
Artigo
Inglês
| MEDLINE | ID: mdl-25981636