Detalhe da pesquisa
1.
Circulating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis.
Blood
; 143(19): 1937-1952, 2024 May 09.
Artigo
Inglês
| MEDLINE | ID: mdl-38446574
2.
ISAnalytics enables longitudinal and high-throughput clonal tracking studies in hematopoietic stem cell gene therapy applications.
Brief Bioinform
; 24(1)2023 01 19.
Artigo
Inglês
| MEDLINE | ID: mdl-36545803
3.
Intrathymic AAV delivery results in therapeutic site-specific integration at TCR loci in mice.
Blood
; 141(19): 2316-2329, 2023 05 11.
Artigo
Inglês
| MEDLINE | ID: mdl-36790505
4.
Removal of innate immune barriers allows efficient transduction of quiescent human hematopoietic stem cells.
Mol Ther
; 32(1): 124-139, 2024 Jan 03.
Artigo
Inglês
| MEDLINE | ID: mdl-37990494
5.
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome.
N Engl J Med
; 385(21): 1929-1940, 2021 11 18.
Artigo
Inglês
| MEDLINE | ID: mdl-34788506
6.
γ-TRIS: a graph-algorithm for comprehensive identification of vector genomic insertion sites.
Bioinformatics
; 36(5): 1622-1624, 2020 03 01.
Artigo
Inglês
| MEDLINE | ID: mdl-31589304
7.
ARPIR: automatic RNA-Seq pipelines with interactive report.
BMC Bioinformatics
; 21(Suppl 19): 574, 2020 Dec 21.
Artigo
Inglês
| MEDLINE | ID: mdl-33349239
8.
VISPA2: a scalable pipeline for high-throughput identification and annotation of vector integration sites.
BMC Bioinformatics
; 18(1): 520, 2017 Nov 25.
Artigo
Inglês
| MEDLINE | ID: mdl-29178837
9.
adLIMS: a customized open source software that allows bridging clinical and basic molecular research studies.
BMC Bioinformatics
; 16 Suppl 9: S5, 2015.
Artigo
Inglês
| MEDLINE | ID: mdl-26051409
10.
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID.
Nat Commun
; 15(1): 3662, 2024 Apr 30.
Artigo
Inglês
| MEDLINE | ID: mdl-38688902
11.
InCliniGene enables high-throughput and comprehensive in vivo clonal tracking toward clinical genomics data integration.
Database (Oxford)
; 20232023 11 02.
Artigo
Inglês
| MEDLINE | ID: mdl-37935583
12.
IL-3-zetakine combined with a CD33 costimulatory receptor as a dual CAR approach for safer and selective targeting of AML.
Blood Adv
; 7(12): 2855-2871, 2023 Jun 27.
Artigo
Inglês
| MEDLINE | ID: mdl-36521101
13.
SiCoDEA: A Simple, Fast and Complete App for Analyzing the Effect of Individual Drugs and Their Combinations.
Biomolecules
; 12(7)2022 06 28.
Artigo
Inglês
| MEDLINE | ID: mdl-35883460
14.
Prolonged XPO1 inhibition is essential for optimal antileukemic activity in NPM1-mutated AML.
Blood Adv
; 6(22): 5938-5949, 2022 11 22.
Artigo
Inglês
| MEDLINE | ID: mdl-36037515
15.
Retrieval of vector integration sites from cell-free DNA.
Nat Med
; 27(8): 1458-1470, 2021 08.
Artigo
Inglês
| MEDLINE | ID: mdl-34140705
16.
Dactinomycin induces complete remission associated with nucleolar stress response in relapsed/refractory NPM1-mutated AML.
Leukemia
; 35(9): 2552-2562, 2021 09.
Artigo
Inglês
| MEDLINE | ID: mdl-33654209
17.
Bcor deficiency perturbs erythro-megakaryopoiesis and cooperates with Dnmt3a loss in acute erythroid leukemia onset in mice.
Leukemia
; 35(7): 1949-1963, 2021 07.
Artigo
Inglês
| MEDLINE | ID: mdl-33159179
18.
Assessing the Impact of Cyclosporin A on Lentiviral Transduction and Preservation of Human Hematopoietic Stem Cells in Clinically Relevant Ex Vivo Gene Therapy Settings.
Hum Gene Ther
; 30(9): 1133-1146, 2019 09.
Artigo
Inglês
| MEDLINE | ID: mdl-31037976
19.
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia.
Nat Med
; 25(2): 234-241, 2019 02.
Artigo
Inglês
| MEDLINE | ID: mdl-30664781
20.
Preclinical Testing of the Safety and Tolerability of Lentiviral Vector-Mediated Above-Normal Alpha-L-Iduronidase Expression in Murine and Human Hematopoietic Cells Using Toxicology and Biodistribution Good Laboratory Practice Studies.
Hum Gene Ther
; 27(10): 813-829, 2016 10.
Artigo
Inglês
| MEDLINE | ID: mdl-27431943