Detalhe da pesquisa
1.
Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A.
N Engl J Med
; 385(21): 1961-1973, 2021 11 18.
Artigo
Inglês
| MEDLINE | ID: mdl-34788507
2.
Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.
N Engl J Med
; 377(23): 2215-2227, 2017 12 07.
Artigo
Inglês
| MEDLINE | ID: mdl-29211678
3.
FLI1 level during megakaryopoiesis affects thrombopoiesis and platelet biology.
Blood
; 129(26): 3486-3494, 2017 06 29.
Artigo
Inglês
| MEDLINE | ID: mdl-28432223
4.
Comparative analysis of human ex vivo-generated platelets vs megakaryocyte-generated platelets in mice: a cautionary tale.
Blood
; 125(23): 3627-36, 2015 Jun 04.
Artigo
Inglês
| MEDLINE | ID: mdl-25852052
5.
High-level transgene expression in induced pluripotent stem cell-derived megakaryocytes: correction of Glanzmann thrombasthenia.
Blood
; 123(5): 753-7, 2014 Jan 30.
Artigo
Inglês
| MEDLINE | ID: mdl-24335497
6.
Challenges and promises for the development of donor-independent platelet transfusions.
Blood
; 121(17): 3319-24, 2013 Apr 25.
Artigo
Inglês
| MEDLINE | ID: mdl-23321255
7.
Patient-derived induced pluripotent stem cells recapitulate hematopoietic abnormalities of juvenile myelomonocytic leukemia.
Blood
; 121(24): 4925-9, 2013 Jun 13.
Artigo
Inglês
| MEDLINE | ID: mdl-23620576
8.
Clonal genetic and hematopoietic heterogeneity among human-induced pluripotent stem cell lines.
Blood
; 122(12): 2047-51, 2013 Sep 19.
Artigo
Inglês
| MEDLINE | ID: mdl-23940280
9.
A(nother) day in the life of neonatal platelets.
Blood
; 123(22): 3372-3, 2014 May 29.
Artigo
Inglês
| MEDLINE | ID: mdl-24876525
10.
Infused factor VIII-expressing platelets or megakaryocytes as a novel therapeutic strategy for hemophilia A.
Blood Adv
; 3(9): 1368-1378, 2019 05 14.
Artigo
Inglês
| MEDLINE | ID: mdl-31036722
11.
Generation of poikiloderma with neutropenia (PN) induced pluripotent stem cells (iPSCs).
Stem Cell Res
; 15(3): 595-7, 2015 Nov.
Artigo
Inglês
| MEDLINE | ID: mdl-26987923
12.
Inducible Gata1 suppression expands megakaryocyte-erythroid progenitors from embryonic stem cells.
J Clin Invest
; 125(6): 2369-74, 2015 Jun.
Artigo
Inglês
| MEDLINE | ID: mdl-25961454
13.
Efficient iPS cell generation from blood using episomes and HDAC inhibitors.
J Vis Exp
; (92): e52009, 2014 Oct 28.
Artigo
Inglês
| MEDLINE | ID: mdl-25408260
14.
The negative impact of Wnt signaling on megakaryocyte and primitive erythroid progenitors derived from human embryonic stem cells.
Stem Cell Res
; 12(2): 441-51, 2014 Mar.
Artigo
Inglês
| MEDLINE | ID: mdl-24412757
15.
Novel C16orf57 mutations in patients with Poikiloderma with Neutropenia: bioinformatic analysis of the protein and predicted effects of all reported mutations.
Orphanet J Rare Dis
; 7: 7, 2012 Jan 23.
Artigo
Inglês
| MEDLINE | ID: mdl-22269211