Detalhe da pesquisa
1.
Engineered lentivirus-derived nanoparticles (LVNPs) for delivery of CRISPR/Cas ribonucleoprotein complexes supporting base editing, prime editing and in vivo gene modification.
Nucleic Acids Res
; 51(18): 10059-10074, 2023 Oct 13.
Artigo
Inglês
| MEDLINE | ID: mdl-37678882
2.
pegIT - a web-based design tool for prime editing.
Nucleic Acids Res
; 49(W1): W505-W509, 2021 07 02.
Artigo
Inglês
| MEDLINE | ID: mdl-34060619
3.
Delivering genes with human immunodeficiency virus-derived vehicles: still state-of-the-art after 25 years.
J Biomed Sci
; 29(1): 79, 2022 Oct 09.
Artigo
Inglês
| MEDLINE | ID: mdl-36209077
4.
Prime editing in hematopoietic stem cells-From ex vivo to in vivo CRISPR-based treatment of blood disorders.
Front Genome Ed
; 5: 1148650, 2023.
Artigo
Inglês
| MEDLINE | ID: mdl-36969373
5.
piggyPrime: High-Efficacy Prime Editing in Human Cells Using piggyBac-Based DNA Transposition.
Front Genome Ed
; 3: 786893, 2021.
Artigo
Inglês
| MEDLINE | ID: mdl-34870275