ß-Sarcoglycan gene transfer decreases fibrosis and restores force in LGMD2E mice.

Pozsgai, E R; Griffin, D A; Heller, K N; Mendell, J R; Rodino-Klapac, L R

Pozsgai, E R; Griffin, D A; Heller, K N; Mendell, J R; Rodino-Klapac, L R.

Pozsgai ER; Biomedical Sciences Graduate Program, The Ohio State University, Columbus, OH, USA.
Griffin DA; Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH, USA.
Heller KN; Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH, USA.
Mendell JR; Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH, USA.
Rodino-Klapac LR; Molecular, Cellular and Developmental Biology Graduate Program, The Ohio State University, Columbus, OH, USA.

Gene Ther ; 23(1): 57-66, 2016 Jan.

Article en En | MEDLINE | ID: mdl-26214262

Asunto(s)

Terapia Genética/métodos; Músculo Esquelético/efectos de los fármacos; Sarcoglicanopatías/terapia; Sarcoglicanos/genética; Animales; Dependovirus/genética; Modelos Animales de Enfermedad; Femenino; Fibrosis/genética; Fibrosis/terapia; Técnicas de Transferencia de Gen; Vectores Genéticos; Humanos; Masculino; Ratones; Ratones Noqueados; Músculo Esquelético/fisiopatología; Distrofias Musculares/genética; Distrofias Musculares/terapia; Mutación; Sarcoglicanopatías/genética; Sarcoglicanos/metabolismo

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Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Terapia Genética / Músculo Esquelético / Sarcoglicanos / Sarcoglicanopatías Límite: Animals / Female / Humans / Male Idioma: En Año: 2016 Tipo del documento: Article

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