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A clinical trial of safety and tolerability for the selective dopamine D1 receptor antagonist ecopipam in patients with Lesch-Nyhan disease.
Khasnavis, Tanya; Reiner, Gail; Sommerfeld, Barbara; Nyhan, William L; Chipkin, Richard; Jinnah, H A.
  • Khasnavis T; Department of Neurology, Emory University, Atlanta, GA 30322, USA.
  • Reiner G; Department of Pediatrics, University of California San Diego, La Jolla, CA, USA.
  • Sommerfeld B; Department of Neurology, Emory University, Atlanta, GA 30322, USA.
  • Nyhan WL; Department of Pediatrics, University of California San Diego, La Jolla, CA, USA.
  • Chipkin R; Psyadon Pharmaceuticals, 20451 Seneca Meadows Parkway, Germantown, MD 20876, USA.
  • Jinnah HA; Department of Neurology, Emory University, Atlanta, GA 30322, USA; Department of Human Genetics, Emory University, Atlanta, GA 30322, USA; Department of Pediatrics, Emory University, Atlanta, GA 30322, USA. Electronic address: hjinnah@emory.edu.
Mol Genet Metab ; 117(4): 401-6, 2016 Apr.
Article en En | MEDLINE | ID: mdl-26922636

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Benzazepinas / Receptores de Dopamina D1 / Antagonistas de Dopamina / Síndrome de Lesch-Nyhan Tipo de estudio: Diagnostic_studies Límite: Adolescent / Adult / Child / Humans / Male / Middle aged Idioma: En Año: 2016 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Benzazepinas / Receptores de Dopamina D1 / Antagonistas de Dopamina / Síndrome de Lesch-Nyhan Tipo de estudio: Diagnostic_studies Límite: Adolescent / Adult / Child / Humans / Male / Middle aged Idioma: En Año: 2016 Tipo del documento: Article