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High-Throughput Screening for Readthrough Modulators of CFTR PTC Mutations.
Liang, Feng; Shang, Haibo; Jordan, Nikole J; Wong, Eric; Mercadante, Dayna; Saltz, Josef; Mahiou, Jerome; Bihler, Hermann J; Mense, Martin.
  • Liang F; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
  • Shang H; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
  • Jordan NJ; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
  • Wong E; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
  • Mercadante D; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
  • Saltz J; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
  • Mahiou J; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
  • Bihler HJ; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
  • Mense M; 1 CFFT Lab, Cystic Fibrosis Foundation Therapeutics, Lexington, MA, USA.
SLAS Technol ; 22(3): 315-324, 2017 06.
Article en En | MEDLINE | ID: mdl-28376702

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Transcripción Genética / Codón sin Sentido / Regulador de Conductancia de Transmembrana de Fibrosis Quística / Fibrosis Quística / Evaluación Preclínica de Medicamentos Tipo de estudio: Diagnostic_studies / Screening_studies Límite: Humans Idioma: En Año: 2017 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Transcripción Genética / Codón sin Sentido / Regulador de Conductancia de Transmembrana de Fibrosis Quística / Fibrosis Quística / Evaluación Preclínica de Medicamentos Tipo de estudio: Diagnostic_studies / Screening_studies Límite: Humans Idioma: En Año: 2017 Tipo del documento: Article