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Testing of therapies in a novel nebulin nemaline myopathy model demonstrate a lack of efficacy.
Sztal, Tamar E; McKaige, Emily A; Williams, Caitlin; Oorschot, Viola; Ramm, Georg; Bryson-Richardson, Robert J.
  • Sztal TE; School of Biological Sciences, Monash University, Melbourne, Australia.
  • McKaige EA; School of Biological Sciences, Monash University, Melbourne, Australia.
  • Williams C; School of Biological Sciences, Monash University, Melbourne, Australia.
  • Oorschot V; Monash Ramaciotti Centre for Cryo Electron Microscopy, Monash University, Melbourne, VIC, 3800, Australia.
  • Ramm G; Monash Ramaciotti Centre for Cryo Electron Microscopy, Monash University, Melbourne, VIC, 3800, Australia.
  • Bryson-Richardson RJ; Department of Biochemistry and Molecular Biology, Monash University, Melbourne, Australia.
Acta Neuropathol Commun ; 6(1): 40, 2018 05 30.
Article en En | MEDLINE | ID: mdl-29848386

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Miopatías Nemalínicas / Músculo Esquelético / Proteínas Musculares / Mutación Límite: Animals Idioma: En Año: 2018 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Miopatías Nemalínicas / Músculo Esquelético / Proteínas Musculares / Mutación Límite: Animals Idioma: En Año: 2018 Tipo del documento: Article