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mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency.
Cao, Jingsong; An, Ding; Galduroz, Mikel; Zhuo, Jenny; Liang, Shi; Eybye, Marianne; Frassetto, Andrea; Kuroda, Eishi; Funahashi, Aki; Santana, Jordan; Mihai, Cosmin; Benenato, Kerry E; Kumarasinghe, E Sathyajith; Sabnis, Staci; Salerno, Timothy; Coughlan, Kimberly; Miracco, Edward J; Levy, Becca; Besin, Gilles; Schultz, Joshua; Lukacs, Christine; Guey, Lin; Finn, Patrick; Furukawa, Tatsuhiko; Giangrande, Paloma H; Saheki, Takeyori; Martini, Paolo G V.
  • Cao J; Moderna, Inc., Cambridge, MA, USA.
  • An D; Moderna, Inc., Cambridge, MA, USA.
  • Galduroz M; Moderna, Inc., Cambridge, MA, USA.
  • Zhuo J; Moderna, Inc., Cambridge, MA, USA.
  • Liang S; Moderna, Inc., Cambridge, MA, USA.
  • Eybye M; Moderna, Inc., Cambridge, MA, USA.
  • Frassetto A; Moderna, Inc., Cambridge, MA, USA.
  • Kuroda E; Department of Molecular Oncology, Kagoshima University, Kagoshima, Japan.
  • Funahashi A; Department of Molecular Oncology, Kagoshima University, Kagoshima, Japan.
  • Santana J; Moderna, Inc., Cambridge, MA, USA.
  • Mihai C; Moderna, Inc., Cambridge, MA, USA.
  • Benenato KE; Moderna, Inc., Cambridge, MA, USA.
  • Kumarasinghe ES; Moderna, Inc., Cambridge, MA, USA.
  • Sabnis S; Moderna, Inc., Cambridge, MA, USA.
  • Salerno T; Moderna, Inc., Cambridge, MA, USA.
  • Coughlan K; Moderna, Inc., Cambridge, MA, USA.
  • Miracco EJ; Moderna, Inc., Cambridge, MA, USA.
  • Levy B; Moderna, Inc., Cambridge, MA, USA.
  • Besin G; Moderna, Inc., Cambridge, MA, USA.
  • Schultz J; Moderna, Inc., Cambridge, MA, USA.
  • Lukacs C; Moderna, Inc., Cambridge, MA, USA.
  • Guey L; Moderna, Inc., Cambridge, MA, USA.
  • Finn P; Moderna, Inc., Cambridge, MA, USA.
  • Furukawa T; Department of Molecular Oncology, Kagoshima University, Kagoshima, Japan.
  • Giangrande PH; Moderna, Inc., Cambridge, MA, USA.
  • Saheki T; Department of Molecular Oncology, Kagoshima University, Kagoshima, Japan.
  • Martini PGV; Moderna, Inc., Cambridge, MA, USA. Electronic address: paolo.martini@modernatx.com.
Mol Ther ; 27(7): 1242-1251, 2019 07 03.
Article en En | MEDLINE | ID: mdl-31056400

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: ARN Mensajero / Terapia Genética / Sistemas de Liberación de Medicamentos / Citrulinemia / Proteínas de Transporte de Membrana Mitocondrial Límite: Animals / Humans Idioma: En Año: 2019 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: ARN Mensajero / Terapia Genética / Sistemas de Liberación de Medicamentos / Citrulinemia / Proteínas de Transporte de Membrana Mitocondrial Límite: Animals / Humans Idioma: En Año: 2019 Tipo del documento: Article