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Complement blockade for TA-TMA: lessons learned from a large pediatric cohort treated with eculizumab.
Jodele, Sonata; Dandoy, Christopher E; Lane, Adam; Laskin, Benjamin L; Teusink-Cross, Ashley; Myers, Kasiani C; Wallace, Gregory; Nelson, Adam; Bleesing, Jack; Chima, Ranjit S; Hirsch, Russel; Ryan, Thomas D; Benoit, Stefanie; Mizuno, Kana; Warren, Mikako; Davies, Stella M.
  • Jodele S; Division of Bone Marrow Transplantation and Immune Deficiency, Cancer and Blood Disease Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH.
  • Dandoy CE; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH.
  • Lane A; Division of Bone Marrow Transplantation and Immune Deficiency, Cancer and Blood Disease Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH.
  • Laskin BL; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH.
  • Teusink-Cross A; Division of Bone Marrow Transplantation and Immune Deficiency, Cancer and Blood Disease Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH.
  • Myers KC; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH.
  • Wallace G; Division of Nephrology, Children's Hospital of Philadelphia, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA.
  • Nelson A; Department of Pharmacy.
  • Bleesing J; Division of Bone Marrow Transplantation and Immune Deficiency, Cancer and Blood Disease Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH.
  • Chima RS; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH.
  • Hirsch R; Division of Bone Marrow Transplantation and Immune Deficiency, Cancer and Blood Disease Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH.
  • Ryan TD; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH.
  • Benoit S; Division of Bone Marrow Transplantation and Immune Deficiency, Cancer and Blood Disease Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH.
  • Mizuno K; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH.
  • Warren M; Division of Bone Marrow Transplantation and Immune Deficiency, Cancer and Blood Disease Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH.
  • Davies SM; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH.
Blood ; 135(13): 1049-1057, 2020 03 26.
Article en En | MEDLINE | ID: mdl-31932840

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Proteínas del Sistema Complemento / Trasplante de Células Madre Hematopoyéticas / Inactivadores del Complemento / Microangiopatías Trombóticas / Anticuerpos Monoclonales Humanizados Tipo de estudio: Diagnostic_studies / Etiology_studies / Incidence_studies / Prognostic_studies / Risk_factors_studies Límite: Adolescent / Child / Child, preschool / Female / Humans / Male Idioma: En Año: 2020 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Proteínas del Sistema Complemento / Trasplante de Células Madre Hematopoyéticas / Inactivadores del Complemento / Microangiopatías Trombóticas / Anticuerpos Monoclonales Humanizados Tipo de estudio: Diagnostic_studies / Etiology_studies / Incidence_studies / Prognostic_studies / Risk_factors_studies Límite: Adolescent / Child / Child, preschool / Female / Humans / Male Idioma: En Año: 2020 Tipo del documento: Article