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Optimized Trientine-dihydrochloride Therapy in Pediatric Patients With Wilson Disease: Is Weight-based Dosing Justified?
Mayr, Toni; Ferenci, Peter; Weiler, Markus; Fichtner, Alexander; Mehrabi, Arianeb; Hoffmann, Georg Friedrich; Mohr, Isabelle; Pfeiffenberger, Jan; Weiss, Karl Heinz; Teufel-Schäfer, Ulrike.
  • Mayr T; Department of Gastroenterology and Hepatology, University Hospital Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
  • Ferenci P; Division of Gastroenterology and Hepatology, Department of Internal Medicine III, Medical University of Vienna, Vienna, Austria.
  • Weiler M; Department of Neurology, University Hospital Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
  • Fichtner A; Center for Child and Adolescent Medicine, Division of Pediatric Gastroenterology and Hepatology, University Hospital Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
  • Mehrabi A; Department of General, Visceral, and Transplantation Surgery, University of Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
  • Hoffmann GF; Center for Child and Adolescent Medicine, Division of Pediatric Gastroenterology and Hepatology, University Hospital Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
  • Mohr I; Department of Gastroenterology and Hepatology, University Hospital Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
  • Pfeiffenberger J; Department of Gastroenterology and Hepatology, University Hospital Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
  • Weiss KH; Department of Gastroenterology and Hepatology, University Hospital Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
  • Teufel-Schäfer U; Center for Child and Adolescent Medicine, Division of Pediatric Gastroenterology and Hepatology, University Hospital Heidelberg, Im Neuenheimer Feld, Heidelberg, Germany.
J Pediatr Gastroenterol Nutr ; 72(1): 115-122, 2021 01 01.
Article en En | MEDLINE | ID: mdl-32804908

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Trientina / Degeneración Hepatolenticular Tipo de estudio: Observational_studies Límite: Adolescent / Child / Humans Idioma: En Año: 2021 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Trientina / Degeneración Hepatolenticular Tipo de estudio: Observational_studies Límite: Adolescent / Child / Humans Idioma: En Año: 2021 Tipo del documento: Article