Novel Orthogonally Hydrocarbon-Modified Cell-Penetrating Peptide Nanoparticles Mediate Efficient Delivery of Splice-Switching Antisense Oligonucleotides In Vitro and In Vivo.

Bazaz, Safa; Lehto, Tõnis; Tops, Rahel; Gissberg, Olof; Gupta, Dhanu; Bestas, Burcu; Bost, Jeremy; Wiklander, Oscar P B; Sork, Helena; Zaghloul, Eman M; Mamand, Doste R; Hällbrink, Mattias; Sillard, Rannar; Saher, Osama; Ezzat, Kariem; Smith, C I Edvard; Andaloussi, Samir El; Lehto, Taavi

Bazaz, Safa; Lehto, Tõnis; Tops, Rahel; Gissberg, Olof; Gupta, Dhanu; Bestas, Burcu; Bost, Jeremy; Wiklander, Oscar P B; Sork, Helena; Zaghloul, Eman M; Mamand, Doste R; Hällbrink, Mattias; Sillard, Rannar; Saher, Osama; Ezzat, Kariem; Smith, C I Edvard; Andaloussi, Samir El; Lehto, Taavi.

Bazaz S; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Lehto T; Department of General Biology, Cihan University-Erbil, Kurdistan Region, Erbil 44001, Iraq.
Tops R; Institute of Technology, University of Tartu, Nooruse 1, 50411 Tartu, Estonia.
Gissberg O; Institute of Technology, University of Tartu, Nooruse 1, 50411 Tartu, Estonia.
Gupta D; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Bestas B; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Bost J; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Wiklander OPB; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Sork H; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Zaghloul EM; Institute of Technology, University of Tartu, Nooruse 1, 50411 Tartu, Estonia.
Mamand DR; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Hällbrink M; Department of Pharmaceutics, Faculty of Pharmacy, Alexandria University, El-Khartoum Square, Azareeta, Alexandria 21521, Egypt.
Sillard R; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Saher O; Department of Biomedical Sciences, Cihan University-Erbil, Erbil 44001, Kurdistan Region, Iraq.
Ezzat K; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Smith CIE; PeptiSystems AB, Virdings Allé 22, 75450 Uppsala, Sweden.
Andaloussi SE; Clinical Research Center, Department of Laboratory Medicine, Karolinska Institutet, Karolinska University Hospital Huddinge, 14186 Huddinge, Sweden.
Lehto T; Department of Pharmaceutics and Industrial Pharmacy, Faculty of Pharmacy, Cairo University, Cairo 11562, Egypt.