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Molecular architecture determines brain delivery of a transferrin receptor-targeted lysosomal enzyme.
Arguello, Annie; Mahon, Cathal S; Calvert, Meredith E K; Chan, Darren; Dugas, Jason C; Pizzo, Michelle E; Thomsen, Elliot R; Chau, Roni; Damo, Lorna A; Duque, Joseph; Fang, Meng; Giese, Tina; Kim, Do Jin; Liang, Nicholas; Nguyen, Hoang N; Solanoy, Hilda; Tsogtbaatar, Buyankhishig; Ullman, Julie C; Wang, Junhua; Dennis, Mark S; Diaz, Dolores; Gunasekaran, Kannan; Henne, Kirk R; Lewcock, Joseph W; Sanchez, Pascal E; Troyer, Matthew D; Harris, Jeffrey M; Scearce-Levie, Kimberly; Shan, Lu; Watts, Ryan J; Thorne, Robert G; Henry, Anastasia G; Kariolis, Mihalis S.
  • Arguello A; Denali Therapeutics Inc., South San Francisco, CA.
  • Mahon CS; Denali Therapeutics Inc., South San Francisco, CA.
  • Calvert MEK; Denali Therapeutics Inc., South San Francisco, CA.
  • Chan D; Denali Therapeutics Inc., South San Francisco, CA.
  • Dugas JC; Denali Therapeutics Inc., South San Francisco, CA.
  • Pizzo ME; Denali Therapeutics Inc., South San Francisco, CA.
  • Thomsen ER; Denali Therapeutics Inc., South San Francisco, CA.
  • Chau R; Denali Therapeutics Inc., South San Francisco, CA.
  • Damo LA; Denali Therapeutics Inc., South San Francisco, CA.
  • Duque J; Denali Therapeutics Inc., South San Francisco, CA.
  • Fang M; Denali Therapeutics Inc., South San Francisco, CA.
  • Giese T; Denali Therapeutics Inc., South San Francisco, CA.
  • Kim DJ; Denali Therapeutics Inc., South San Francisco, CA.
  • Liang N; Denali Therapeutics Inc., South San Francisco, CA.
  • Nguyen HN; Denali Therapeutics Inc., South San Francisco, CA.
  • Solanoy H; Denali Therapeutics Inc., South San Francisco, CA.
  • Tsogtbaatar B; Denali Therapeutics Inc., South San Francisco, CA.
  • Ullman JC; Denali Therapeutics Inc., South San Francisco, CA.
  • Wang J; Denali Therapeutics Inc., South San Francisco, CA.
  • Dennis MS; Denali Therapeutics Inc., South San Francisco, CA.
  • Diaz D; Denali Therapeutics Inc., South San Francisco, CA.
  • Gunasekaran K; Denali Therapeutics Inc., South San Francisco, CA.
  • Henne KR; Denali Therapeutics Inc., South San Francisco, CA.
  • Lewcock JW; Denali Therapeutics Inc., South San Francisco, CA.
  • Sanchez PE; Denali Therapeutics Inc., South San Francisco, CA.
  • Troyer MD; Denali Therapeutics Inc., South San Francisco, CA.
  • Harris JM; Denali Therapeutics Inc., South San Francisco, CA.
  • Scearce-Levie K; Denali Therapeutics Inc., South San Francisco, CA.
  • Shan L; Denali Therapeutics Inc., South San Francisco, CA.
  • Watts RJ; Denali Therapeutics Inc., South San Francisco, CA.
  • Thorne RG; Denali Therapeutics Inc., South San Francisco, CA.
  • Henry AG; Department of Pharmaceutics, University of Minnesota, Minneapolis, MN.
  • Kariolis MS; Denali Therapeutics Inc., South San Francisco, CA.
J Exp Med ; 219(3)2022 03 07.
Article en En | MEDLINE | ID: mdl-35226042

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Receptores de Transferrina / Proteínas Recombinantes de Fusión / Mucopolisacaridosis II / Iduronato Sulfatasa Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Año: 2022 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Receptores de Transferrina / Proteínas Recombinantes de Fusión / Mucopolisacaridosis II / Iduronato Sulfatasa Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Año: 2022 Tipo del documento: Article