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Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial.
McDonald, Craig M; Marbán, Eduardo; Hendrix, Suzanne; Hogan, Nathaniel; Ruckdeschel Smith, Rachel; Eagle, Michelle; Finkel, Richard S; Tian, Cuixia; Janas, Joanne; Harmelink, Matthew M; Varadhachary, Arun S; Taylor, Michael D; Hor, Kan N; Mayer, Oscar H; Henricson, Erik K; Furlong, Pat; Ascheim, Deborah D; Rogy, Siegfried; Williams, Paula; Marbán, Linda.
  • McDonald CM; University of California Davis School of Medicine, Sacramento, CA, USA. Electronic address: cmmcdonald@ucdavis.edu.
  • Marbán E; Smidt Heart Institute, Cedars-Sinai Medical Center, Los Angeles, CA, USA.
  • Hendrix S; Pentara, Millcreek, UT, USA.
  • Hogan N; Pentara, Millcreek, UT, USA.
  • Ruckdeschel Smith R; Capricor Therapeutics, Beverly Hills, CA, USA.
  • Eagle M; Atom International, Newcastle upon Tyne, UK.
  • Finkel RS; Nemours Children's Hospital, Orlando, FL, USA; St Jude Children's Research Hospital, Memphis, TN, USA.
  • Tian C; Cincinnati Children's Hospital Medical Center and University of Cincinnati College of Medicine, Cincinnati, OH, USA.
  • Janas J; University of Colorado, Children's Hospital Colorado, Denver, CO, USA.
  • Harmelink MM; Medical College of Wisconsin, Milwaukee, WI, USA.
  • Varadhachary AS; Washington University School of Medicine, St Louis, MO, USA.
  • Taylor MD; Cincinnati Children's Hospital Medical Center and University of Cincinnati College of Medicine, Cincinnati, OH, USA.
  • Hor KN; Nationwide Children's Hospital, Columbus, OH, USA.
  • Mayer OH; Children's Hospital of Philadelphia and University of Pennsylvania, Philadelphia, PA, USA.
  • Henricson EK; University of California Davis School of Medicine, Sacramento, CA, USA.
  • Furlong P; Parent Project Muscular Dystrophy, Hackensack, NJ, USA.
  • Ascheim DD; Capricor Therapeutics, Beverly Hills, CA, USA.
  • Rogy S; Capricor Therapeutics, Beverly Hills, CA, USA.
  • Williams P; Capricor Therapeutics, Beverly Hills, CA, USA.
  • Marbán L; Capricor Therapeutics, Beverly Hills, CA, USA.
Lancet ; 399(10329): 1049-1058, 2022 03 12.
Article en En | MEDLINE | ID: mdl-35279258

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Distrofia Muscular de Duchenne / Cardiomiopatías Tipo de estudio: Clinical_trials / Prognostic_studies Límite: Child / Humans / Male Idioma: En Año: 2022 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Distrofia Muscular de Duchenne / Cardiomiopatías Tipo de estudio: Clinical_trials / Prognostic_studies Límite: Child / Humans / Male Idioma: En Año: 2022 Tipo del documento: Article