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Cross-species evolution of a highly potent AAV variant for therapeutic gene transfer and genome editing.
Gonzalez, Trevor J; Simon, Katherine E; Blondel, Leo O; Fanous, Marco M; Roger, Angela L; Maysonet, Maribel Santiago; Devlin, Garth W; Smith, Timothy J; Oh, Daniel K; Havlik, L Patrick; Castellanos Rivera, Ruth M; Piedrahita, Jorge A; ElMallah, Mai K; Gersbach, Charles A; Asokan, Aravind.
  • Gonzalez TJ; Department of Molecular Genetics and Microbiology, Duke University School of Medicine, Durham, NC, USA.
  • Simon KE; Department of Surgery, Duke University School of Medicine, Durham, NC, USA.
  • Blondel LO; North Carolina State University College of Veterinary Medicine, Raleigh, NC, USA.
  • Fanous MM; Department of Surgery, Duke University School of Medicine, Durham, NC, USA.
  • Roger AL; Department of Surgery, Duke University School of Medicine, Durham, NC, USA.
  • Maysonet MS; Department of Pediatrics, Duke University School of Medicine, Durham, NC, USA.
  • Devlin GW; StrideBio Inc., Research Triangle Park, Durham, NC, USA.
  • Smith TJ; Department of Surgery, Duke University School of Medicine, Durham, NC, USA.
  • Oh DK; Department of Molecular Genetics and Microbiology, Duke University School of Medicine, Durham, NC, USA.
  • Havlik LP; Department of Surgery, Duke University School of Medicine, Durham, NC, USA.
  • Castellanos Rivera RM; Department of Surgery, Duke University School of Medicine, Durham, NC, USA.
  • Piedrahita JA; StrideBio Inc., Research Triangle Park, Durham, NC, USA.
  • ElMallah MK; North Carolina State University College of Veterinary Medicine, Raleigh, NC, USA.
  • Gersbach CA; Department of Pediatrics, Duke University School of Medicine, Durham, NC, USA.
  • Asokan A; Duke Regeneration Center, Duke University School of Medicine, Durham, NC, USA.
Nat Commun ; 13(1): 5947, 2022 10 10.
Article en En | MEDLINE | ID: mdl-36210364

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Dependovirus / Edición Génica Tipo de estudio: Prognostic_studies Límite: Animals / Humans Idioma: En Año: 2022 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Dependovirus / Edición Génica Tipo de estudio: Prognostic_studies Límite: Animals / Humans Idioma: En Año: 2022 Tipo del documento: Article