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IDEAL study: A real-world assessment of pattern of use and clinical outcomes with recombinant coagulation factor IX albumin fusion protein (rIX-FP) in patients with haemophilia B in Italy.
Tagliaferri, Annarita; Molinari, Angelo Claudio; Peyvandi, Flora; Coppola, Antonio; Demartis, Francesco; Biasoli, Chiara; Borchiellini, Alessandra; Cultrera, Dorina; De Cristofaro, Raimondo; Daniele, Filomena; Giordano, Paola; Marchesini, Emanuela; Margaglione, Maurizio; Marino, Renato; Pollio, Berardino; Radossi, Paolo; Santoro, Cristina; Santoro, Rita Carlotta; Siragusa, Sergio; Sottilotta, Gianluca; Tosetto, Alberto; Piscitelli, Lydia; Villa, Maria Rosaria; Zanon, Ezio; Finardi, Adele; Schiavetti, Irene; Vaccari, Daniella; Castaman, Giancarlo.
  • Tagliaferri A; Regional Reference Centre for Inherited Bleeding Disorders, University Hospital of Parma, Parma, Italy.
  • Molinari AC; Regional Reference Centre for Haemorrhagic Diseases, IRCCS Istituto Giannina Gaslini, Genova, Italy.
  • Peyvandi F; Department of Pathophysiology and Transplantation, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Haemophilia and Thrombosis Centre, Università degli Studi di Milano, Milan, Italy.
  • Coppola A; Regional Reference Centre for Inherited Bleeding Disorders, University Hospital of Parma, Parma, Italy.
  • Demartis F; Department of Oncology, Centre for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy.
  • Biasoli C; Haemophilia and Transfusion Centre, "Bufalini" Hospital, Cesena, Italy.
  • Borchiellini A; Regional Reference Centre for Bleeding and Thrombotic Disorders, "Città della Salute e della Scienza" University Hospital, Turin, Italy.
  • Cultrera D; Haemophilia Regional Reference Centre, Haematology Unit, Policlinico "G. Rodolico - S. Marco" Hospital, Catania, Italy.
  • De Cristofaro R; Haemorrhagic and Thrombotic Disease Service, Area of Haematological and Oncological Sciences, IRCCS Fondazione Policlinico Universitario "A. Gemelli", Rome, Italy.
  • Daniele F; Haemostasis and Thrombosis Service, Ospedale Civile dell'Annunziata, Cosenza, Italy.
  • Giordano P; "B. Trambusti" General and Specialised Paediatrics Unit, "Giovanni XXIII" Hospital, University of Bari, Bari, Italy.
  • Marchesini E; Haemophilia Centre, Internal and Cardiovascular Medicine, "Santa Maria della Misericordia" University Hospital, Perugia, Italy.
  • Margaglione M; Department of Clinical and Experimental Medicine, University of Foggia, Foggia, Italy.
  • Marino R; Haemophilia and Thrombosis Centre, University Hospital, Bari, Italy.
  • Pollio B; Regional Reference Centre for Inherited Bleeding and Thrombotic Disorders, Transfusion Medicine, "Regina Margherita" Children Hospital, Turin, Italy.
  • Radossi P; Onco-Haematology Unit, Istituto Oncologico Veneto, Castelfranco Veneto Hospital, Castelfranco Veneto, Italy.
  • Santoro C; Department of Haematology, University Hospital Policlinico Umberto I, Rome, Italy.
  • Santoro RC; Regional Reference Centre for Haemophilia and Coagulation Diseases, Azienda Ospedaliera Pugliese-Ciaccio, Catanzaro, Italy.
  • Siragusa S; Haematology Unit, Thrombosis and Haemostasis Reference Regional Centre, University of Palermo, Palermo, Italy.
  • Sottilotta G; Haemophilia Centre, Grande Ospedale Metropolitano, Reggio Calabria, Italy.
  • Tosetto A; Haematology Department, Haemostasis and Thrombosis Unit, San Bortolo Hospital, Vicenza, Italy.
  • Piscitelli L; SSD Congenital Haemorrhagic Diseases, IRCCS Azienda Ospedaliero-Universitaria di Bologna, Bologna, Italy.
  • Villa MR; Haemophilia and Thrombosis Centre, Haematology Unit, "Ospedale del Mare" Hospital, Naples, Italy.
  • Zanon E; Department of Medicine, Haemophilia Centre, University Hospital of Padua, Padua, Italy.
  • Finardi A; CSL Behring, Milan, Italy.
  • Schiavetti I; Hippocrates Research, Genova, Italy.
  • Vaccari D; Department of Health Sciences, University of Genoa, Genoa, Italy.
  • Castaman G; Hippocrates Research, Genova, Italy.
Haemophilia ; 29(1): 135-144, 2023 Jan.
Article en En | MEDLINE | ID: mdl-36423202

Texto completo: 1 Ejes tematicos: Pesquisa_clinica Banco de datos: MEDLINE Asunto principal: Factor IX / Hemofilia B Tipo de estudio: Observational_studies Límite: Adult / Humans / Male País como asunto: Europa Idioma: En Año: 2023 Tipo del documento: Article

Texto completo: 1 Ejes tematicos: Pesquisa_clinica Banco de datos: MEDLINE Asunto principal: Factor IX / Hemofilia B Tipo de estudio: Observational_studies Límite: Adult / Humans / Male País como asunto: Europa Idioma: En Año: 2023 Tipo del documento: Article