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Effects of switching from imiglucerase to velaglucerase alfa without dose reduction nor wash out in type 1 Gaucher disease.
Serratrice, Christine; Bengherbia, Monia; Alessandrini, Marine; Grosbois, Bernard; Camou, Fabrice; Pers, Yves Marie; Bismuth, Michael; Marie, Isabelle; Belmatoug, Nadia; Berger, Marc.
Afiliação
  • Serratrice C; Department of internal medicine, Hôpital Saint Joseph, Marseille, France. Electronic address: cserratrice@hotmail.fr.
  • Bengherbia M; Referal Center for Lysosomal Diseases, CHU Paris Nord Val de Seine, France.
  • Alessandrini M; EA 3279 Research Unit, Marseille, France.
  • Grosbois B; Department of internal Medicine, CHU Hôpital Sud, Rennes, France.
  • Camou F; Medical Intensive Care Unit, CHU Saint André, Bordeaux, France.
  • Pers YM; Clinical immunology and osteoarticular diseases Therapeutic Unit, CHRU Lapeyronie, Montpellier, France.
  • Bismuth M; Department of gastroenterology, CHU Saint Eloi, Montpellier, France.
  • Marie I; Department of internal Medicine, CHU Rouen, Rouen, France.
  • Belmatoug N; Referal Center for Lysosomal Diseases, CHU Paris Nord Val de Seine, France.
  • Berger M; Department of hematology, CHU Estaing, Clermont Ferrand, France.
Blood Cells Mol Dis ; 53(1-2): 94-6, 2014.
Article em En | MEDLINE | ID: mdl-24411065

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia de Reposição de Enzimas / Doença de Gaucher / Glucosilceramidase Limite: Humans Idioma: En Ano de publicação: 2014 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia de Reposição de Enzimas / Doença de Gaucher / Glucosilceramidase Limite: Humans Idioma: En Ano de publicação: 2014 Tipo de documento: Article