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Measuring clinical effectiveness of medicinal products for the treatment of Duchenne muscular dystrophy.
Lynn, Stephen; Aartsma-Rus, Annemieke; Bushby, Kate; Furlong, Pat; Goemans, Nathalie; De Luca, Annamaria; Mayhew, Anna; McDonald, Craig; Mercuri, Eugenio; Muntoni, Francesco; Pohlschmidt, Marita; Verschuuren, Jan; Voit, Thomas; Vroom, Elizabeth; Wells, Dominic J; Straub, Volker.
Afiliação
  • Lynn S; Newcastle University, Newcastle upon Tyne, UK.
  • Aartsma-Rus A; Newcastle University, Newcastle upon Tyne, UK; Leiden University Medical Centre, Leiden, The Netherlands.
  • Bushby K; Newcastle University, Newcastle upon Tyne, UK.
  • Furlong P; Parent Project Muscular Dystrophy, Hackensack, NJ, USA.
  • Goemans N; University of Leuven, Leuven, Belgium.
  • De Luca A; University of Bari, Bari, Italy.
  • Mayhew A; Newcastle University, Newcastle upon Tyne, UK.
  • McDonald C; University of California Davis, Davis, CA, USA.
  • Mercuri E; Catholic University Rome, Rome, Italy.
  • Muntoni F; University College London, London, UK.
  • Pohlschmidt M; Muscular Dystrophy Campaign, London, UK.
  • Verschuuren J; Leiden University Medical Centre, Leiden, The Netherlands.
  • Voit T; University Pierre et Marie Curie Paris 6, Institut de Myologie, UPMC-INSERM UMR 974, CNRS FRE 3617, GH Pitié-Salpêtrière, Paris, France.
  • Vroom E; Duchenne Parent Project, Amsterdam, The Netherlands.
  • Wells DJ; Royal Veterinary College, London, UK.
  • Straub V; Newcastle University, Newcastle upon Tyne, UK. Electronic address: volker.straub@ncl.ac.uk.
Neuromuscul Disord ; 25(1): 96-105, 2015 Jan.
Article em En | MEDLINE | ID: mdl-25307856

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Avaliação de Processos e Resultados em Cuidados de Saúde / Ensaios Clínicos como Assunto / Distrofia Muscular de Duchenne Limite: Animals / Humans Idioma: En Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Avaliação de Processos e Resultados em Cuidados de Saúde / Ensaios Clínicos como Assunto / Distrofia Muscular de Duchenne Limite: Animals / Humans Idioma: En Ano de publicação: 2015 Tipo de documento: Article