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Velaglucerase alfa (VPRIV) enzyme replacement therapy in patients with Gaucher disease: Long-term data from phase III clinical trials.
Hughes, Derralynn A; Gonzalez, Derlis E; Lukina, Elena A; Mehta, Atul; Kabra, Madhulika; Elstein, Deborah; Kisinovsky, Isaac; Giraldo, Pilar; Bavdekar, Ashish; Hangartner, Thomas N; Wang, Nan; Crombez, Eric; Zimran, Ari.
Afiliação
  • Hughes DA; Department of Haematology, Royal Free Hospital, London, United Kingdom.
  • Gonzalez DE; Department of Haematology, University College London, London, United Kingdom.
  • Lukina EA; Instituto Privado de Hematología e Investigación Clínica - IPHIC, Asunción, Paraguay.
  • Mehta A; Department of Orphan Diseases, Hematology Research Center, Moscow, Russia.
  • Kabra M; Department of Haematology, Royal Free Hospital, London, United Kingdom.
  • Elstein D; Department of Haematology, University College London, London, United Kingdom.
  • Kisinovsky I; Pediatrics Department, All India Institute of Medical Sciences, New Delhi, India.
  • Giraldo P; Gaucher Clinic, Shaare Zedek Medical Center, affiliated with the Hebrew University-Hadassah Medical School, Jerusalem, Israel.
  • Bavdekar A; Hematology Department, Your Health SA, Buenos Aires, Argentina.
  • Hangartner TN; Medicina Metabólica Hereditaria, Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Zaragoza, Spain.
  • Wang N; Grupo de Estudio de Enfermedades Hematologícas y Metabolicas, Hospital Universitario Miguel Servet, Zaragoza, Spain.
  • Crombez E; Pediatric Gastroenterology Department, King Edward Memorial Hospital Research Centre, Pune, India.
  • Zimran A; Department of Biomedical, Industrial, & Human Factors Engineering, Wright State University, Dayton, Ohio.
Am J Hematol ; 90(7): 584-91, 2015 Jul.
Article em En | MEDLINE | ID: mdl-25801797

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia de Reposição de Enzimas / Doença de Gaucher / Glucosilceramidase Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia de Reposição de Enzimas / Doença de Gaucher / Glucosilceramidase Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2015 Tipo de documento: Article