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Reducing GBA2 Activity Ameliorates Neuropathology in Niemann-Pick Type C Mice.
Marques, André R A; Aten, Jan; Ottenhoff, Roelof; van Roomen, Cindy P A A; Herrera Moro, Daniela; Claessen, Nike; Vinueza Veloz, María Fernanda; Zhou, Kuikui; Lin, Zhanmin; Mirzaian, Mina; Boot, Rolf G; De Zeeuw, Chris I; Overkleeft, Herman S; Yildiz, Yildiz; Aerts, Johannes M F G.
Afiliação
  • Marques AR; Department of Medical Biochemistry, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands.
  • Aten J; Department of Pathology, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands.
  • Ottenhoff R; Department of Medical Biochemistry, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands.
  • van Roomen CP; Department of Medical Biochemistry, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands.
  • Herrera Moro D; Department of Medical Biochemistry, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands.
  • Claessen N; Department of Pathology, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands.
  • Vinueza Veloz MF; Department of Neuroscience, Erasmus MC, 3000 CA, Rotterdam, The Netherlands.
  • Zhou K; Department of Neuroscience, Erasmus MC, 3000 CA, Rotterdam, The Netherlands.
  • Lin Z; Department of Neuroscience, Erasmus MC, 3000 CA, Rotterdam, The Netherlands.
  • Mirzaian M; Department of Medical Biochemistry, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands.
  • Boot RG; Department of Medical Biochemistry, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands.
  • De Zeeuw CI; Department of Neuroscience, Erasmus MC, 3000 CA, Rotterdam, The Netherlands; Netherlands Institute for Neuroscience, Royal Dutch Academy of Arts & Sciences, 1105 BA, Amsterdam, The Netherlands.
  • Overkleeft HS; Leiden Institute of Chemistry, Leiden University, 2300 RA, Leiden, The Netherlands.
  • Yildiz Y; Department of Internal Medicine, Hospital of Bregenz, 6900, Bregenz, Austria.
  • Aerts JM; Department of Medical Biochemistry, Academic Medical Center, 1105 AZ, Amsterdam, The Netherlands; Leiden Institute of Chemistry, Leiden University, 2300 RA, Leiden, The Netherlands.
PLoS One ; 10(8): e0135889, 2015.
Article em En | MEDLINE | ID: mdl-26275242

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Beta-Glucosidase / Doença de Niemann-Pick Tipo C / Glucosilceramidas Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Animals Idioma: En Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Beta-Glucosidase / Doença de Niemann-Pick Tipo C / Glucosilceramidas Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Animals Idioma: En Ano de publicação: 2015 Tipo de documento: Article