Evaluation of 2'-Deoxy-2'-fluoro Antisense Oligonucleotides for Exon Skipping in Duchenne Muscular Dystrophy.

Jirka, Silvana M G; Tanganyika-de Winter, Christa L; Boertje-van der Meulen, Joke W; van Putten, Maaike; Hiller, Monika; Vermue, Rick; de Visser, Peter C; Aartsma-Rus, Annemieke.

Afiliação

Jirka SM; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
Tanganyika-de Winter CL; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
Boertje-van der Meulen JW; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
van Putten M; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
Hiller M; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
Vermue R; BioMarin, Leiden, The Netherlands.
de Visser PC; BioMarin, Leiden, The Netherlands.
Aartsma-Rus A; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.

Mol Ther Nucleic Acids ; 4: e265, 2015 Dec 01.

Article em En | MEDLINE | ID: mdl-26623937

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2015 Tipo de documento: Article