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A Novel Family of Small Molecules that Enhance the Intracellular Delivery and Pharmacological Effectiveness of Antisense and Splice Switching Oligonucleotides.
Wang, Ling; Ariyarathna, Yamuna; Ming, Xin; Yang, Bing; James, Lindsey I; Kreda, Silvia M; Porter, Melissa; Janzen, William; Juliano, Rudolph L.
Afiliação
  • Wang L; Initos Pharmaceuticals LLC, Eshelman Institute for Innovation MicroIncubator, CB# 7564, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
  • Ariyarathna Y; UNC Eshelman School of Pharmacy, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
  • Ming X; UNC Eshelman School of Pharmacy, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
  • Yang B; UNC Eshelman School of Pharmacy, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
  • James LI; UNC Eshelman School of Pharmacy, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
  • Kreda SM; UNC Cystic Fibrosis Center and Marsico Lung Institute, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
  • Porter M; UNC Eshelman School of Pharmacy, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
  • Janzen W; UNC Eshelman School of Pharmacy, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
  • Juliano RL; Initos Pharmaceuticals LLC, Eshelman Institute for Innovation MicroIncubator, CB# 7564, University of North Carolina , Chapel Hill, North Carolina 27599, United States.
ACS Chem Biol ; 12(8): 1999-2007, 2017 08 18.
Article em En | MEDLINE | ID: mdl-28703575

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Oligonucleotídeos Antissenso / Bibliotecas de Moléculas Pequenas Limite: Animals / Humans Idioma: En Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Oligonucleotídeos Antissenso / Bibliotecas de Moléculas Pequenas Limite: Animals / Humans Idioma: En Ano de publicação: 2017 Tipo de documento: Article