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Evaluation of tolerance to lentiviral LV-RPE65 gene therapy vector after subretinal delivery in non-human primates.
Matet, Alexandre; Kostic, Corinne; Bemelmans, Alexis-Pierre; Moulin, Alexandre; Rosolen, Serge G; Martin, Samia; Mavilio, Fulvio; Amirjanians, Vazrik; Stieger, Knut; Lorenz, Birgit; Behar-Cohen, Francine; Arsenijevic, Yvan.
Afiliação
  • Matet A; Unit of Retinal Degeneration and Regeneration, Department of Ophthalmology, University of Lausanne, Jules-Gonin Eye Hospital, Fondation Asile des Aveugles, Lausanne, Switzerland.
  • Kostic C; Unit of Retinal Degeneration and Regeneration, Department of Ophthalmology, University of Lausanne, Jules-Gonin Eye Hospital, Fondation Asile des Aveugles, Lausanne, Switzerland. Electronic address: corinne.kostic@fa2.ch.
  • Bemelmans AP; Commissariat à l'Energie Atomique et aux Energies Alternatives (CEA), Direction de la Recherche Fondamentale (DRF), Institut d'Imagerie Biomédicale (I2BM), Molecular Imaging Research Center (MIRCen), Fontenay-aux-Roses, France; Centre National de la Recherche Scientifique (CNRS), Université Paris-Su
  • Moulin A; Pathology Unit, Department of Ophthalmology, University of Lausanne, Jules-Gonin Eye Hospital, Fondation Asile des Aveugles, Lausanne, Switzerland.
  • Rosolen SG; Clinique Vétérinaire Voltaire, Asnières, France; UPMC Univ Paris 06, UMR_ S 968, Centre de Recherche Institut de la Vision, Paris, France.
  • Martin S; Genethon, Evry, France.
  • Mavilio F; Genethon, Evry, France.
  • Amirjanians V; Department of Ophthalmology, Justus-Liebig-University Giessen, Giessen, Germany.
  • Stieger K; Department of Ophthalmology, Justus-Liebig-University Giessen, Giessen, Germany.
  • Lorenz B; Department of Ophthalmology, Justus-Liebig-University Giessen, Giessen, Germany.
  • Behar-Cohen F; Unit of Retinal Degeneration and Regeneration, Department of Ophthalmology, University of Lausanne, Jules-Gonin Eye Hospital, Fondation Asile des Aveugles, Lausanne, Switzerland; Inserm U1138, Team 17, From Physiopathology of Ocular Diseases to Clinical Development, Université Paris Descartes Sorbon
  • Arsenijevic Y; Unit of Retinal Degeneration and Regeneration, Department of Ophthalmology, University of Lausanne, Jules-Gonin Eye Hospital, Fondation Asile des Aveugles, Lausanne, Switzerland. Electronic address: yvan.arsenijevic@fa2.ch.
Transl Res ; 188: 40-57.e4, 2017 10.
Article em En | MEDLINE | ID: mdl-28754419

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Técnicas de Transferência de Genes / Lentivirus / Receptores Acoplados a Proteínas G / Proteínas do Olho / Vetores Genéticos Limite: Animals Idioma: En Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Técnicas de Transferência de Genes / Lentivirus / Receptores Acoplados a Proteínas G / Proteínas do Olho / Vetores Genéticos Limite: Animals Idioma: En Ano de publicação: 2017 Tipo de documento: Article