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Safety of rAAV2/2-ND4 Gene Therapy for Leber Hereditary Optic Neuropathy.
Vignal, Catherine; Uretsky, Scott; Fitoussi, Serge; Galy, Anne; Blouin, Laure; Girmens, Jean-François; Bidot, Samuel; Thomasson, Nitza; Bouquet, Céline; Valero, Sonia; Meunier, Sandrine; Combal, Jean-Philippe; Gilly, Bernard; Katz, Barrett; Sahel, José-Alain.
Afiliação
  • Vignal C; Centre d'Investigation Clinique 1423, Inserm-DGOS, Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts, Paris, France; Rothschild Ophthalmology Foundation Hospital, Paris, France.
  • Uretsky S; GenSight Biologics, Paris, France.
  • Fitoussi S; GenSight Biologics, Paris, France.
  • Galy A; GenSight Biologics, Paris, France.
  • Blouin L; GenSight Biologics, Paris, France.
  • Girmens JF; Centre d'Investigation Clinique 1423, Inserm-DGOS, Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts, Paris, France.
  • Bidot S; Centre d'Investigation Clinique 1423, Inserm-DGOS, Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts, Paris, France; Rothschild Ophthalmology Foundation Hospital, Paris, France.
  • Thomasson N; GenSight Biologics, Paris, France.
  • Bouquet C; GenSight Biologics, Paris, France.
  • Valero S; GenSight Biologics, Paris, France.
  • Meunier S; GenSight Biologics, Paris, France.
  • Combal JP; GenSight Biologics, Paris, France.
  • Gilly B; GenSight Biologics, Paris, France.
  • Katz B; GenSight Biologics, Paris, France; GenSight Biologics Inc., New York, New York. Electronic address: bkatz@gensight-biologics.com.
  • Sahel JA; Centre d'Investigation Clinique 1423, Inserm-DGOS, Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts, Paris, France; Rothschild Ophthalmology Foundation Hospital, Paris, France; Sorbonne Université, INSERM, CNRS, Institut de la Vision, Paris, France; Department of Ophthalmology, Universi
Ophthalmology ; 125(6): 945-947, 2018 06.
Article em En | MEDLINE | ID: mdl-29426586

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Dependovirus / Atrofia Óptica Hereditária de Leber / Vetores Genéticos / NADH Desidrogenase Tipo de estudo: Clinical_trials / Observational_studies / Risk_factors_studies Limite: Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Dependovirus / Atrofia Óptica Hereditária de Leber / Vetores Genéticos / NADH Desidrogenase Tipo de estudo: Clinical_trials / Observational_studies / Risk_factors_studies Limite: Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2018 Tipo de documento: Article