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Advanced siRNA Designs Further Improve In Vivo Performance of GalNAc-siRNA Conjugates.
Foster, Donald J; Brown, Christopher R; Shaikh, Sarfraz; Trapp, Casey; Schlegel, Mark K; Qian, Kun; Sehgal, Alfica; Rajeev, Kallanthottathil G; Jadhav, Vasant; Manoharan, Muthiah; Kuchimanchi, Satya; Maier, Martin A; Milstein, Stuart.
Afiliação
  • Foster DJ; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Brown CR; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Shaikh S; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Trapp C; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Schlegel MK; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Qian K; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Sehgal A; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Rajeev KG; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Jadhav V; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Manoharan M; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Kuchimanchi S; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Maier MA; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Milstein S; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA. Electronic address: smilstein@alnylam.com.
Mol Ther ; 26(3): 708-717, 2018 03 07.
Article em En | MEDLINE | ID: mdl-29456020

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Acetilgalactosamina / RNA Interferente Pequeno / Interferência de RNA Limite: Animals Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Acetilgalactosamina / RNA Interferente Pequeno / Interferência de RNA Limite: Animals Idioma: En Ano de publicação: 2018 Tipo de documento: Article