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Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis.
Tucci, Francesca; Calbi, Valeria; Barzaghi, Federica; Migliavacca, Maddalena; Ferrua, Francesca; Bernardo, Maria Ester; Canarutto, Daniele; Consiglieri, Giulia; Recupero, Salvatore; Calzatini, Francesco; Gabaldo, Michela; Lucano, Caterina; Casiraghi, Miriam; Darin, Silvia; Dionisio, Francesca; Marktel, Sarah; Cestone, Enza; Finazzi, Renato; Mieli-Vergani, Giorgina; Boeri, Enzo; Appleby, Jonathan; Abd Elaziz, Dalia; Ciceri, Fabio; Aiuti, Alessandro; Cicalese, Maria Pia.
Afiliação
  • Tucci F; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Calbi V; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Barzaghi F; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Migliavacca M; Tor Vergata University, Rome, Italy.
  • Ferrua F; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Bernardo ME; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Canarutto D; San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Consiglieri G; Vita Salute San Raffaele University, Milan, Italy.
  • Recupero S; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Calzatini F; San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Gabaldo M; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Lucano C; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Casiraghi M; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Darin S; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Dionisio F; San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Marktel S; San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Cestone E; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Finazzi R; San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Mieli-Vergani G; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Boeri E; San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Appleby J; San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Abd Elaziz D; Haematology and Bone Marrow Transplantation Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Ciceri F; Dermatology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Aiuti A; Unit of Hepatology, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Cicalese MP; MowatLabs, Pediatric Liver, GI & Nutrition Centre, King's College Hospital, London, UK.
Hepatology ; 68(6): 2434-2437, 2018 12.
Article em En | MEDLINE | ID: mdl-30014500

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Antivirais / Uridina Monofosfato / Benzimidazóis / Terapia Genética / Adenosina Desaminase / Imunodeficiência Combinada Severa / Hepatite C / Agamaglobulinemia / Fluorenos Limite: Humans / Infant / Male Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Antivirais / Uridina Monofosfato / Benzimidazóis / Terapia Genética / Adenosina Desaminase / Imunodeficiência Combinada Severa / Hepatite C / Agamaglobulinemia / Fluorenos Limite: Humans / Infant / Male Idioma: En Ano de publicação: 2018 Tipo de documento: Article