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Intramuscular delivery of HGF-expressing recombinant AAV improves muscle integrity and alleviates neurological symptoms in the nerve crush and SOD1-G93A transgenic mouse models.
Lee, Sang Hwan; Lee, Nayeon; Kim, Subin; Lee, Junghun; Choi, Wooshik; Yu, Seung Shin; Kim, Jin Hong; Kim, Sunyoung.
Afiliação
  • Lee SH; School of Biological Sciences, Seoul National University, Seoul, 08826, South Korea.
  • Lee N; R&D Center for Innovative Medicines, Helixmith Co., Ltd, Seoul, 08826, South Korea; School of Biological Sciences, Seoul National University, Seoul, 08826, South Korea.
  • Kim S; R&D Center for Innovative Medicines, Helixmith Co., Ltd, Seoul, 08826, South Korea.
  • Lee J; R&D Center for Innovative Medicines, Helixmith Co., Ltd, Seoul, 08826, South Korea.
  • Choi W; School of Biological Sciences, Seoul National University, Seoul, 08826, South Korea.
  • Yu SS; R&D Center for Innovative Medicines, Helixmith Co., Ltd, Seoul, 08826, South Korea.
  • Kim JH; School of Biological Sciences, Seoul National University, Seoul, 08826, South Korea.
  • Kim S; R&D Center for Innovative Medicines, Helixmith Co., Ltd, Seoul, 08826, South Korea. Electronic address: sk@helixmith.com.
Biochem Biophys Res Commun ; 517(3): 452-457, 2019 09 24.
Article em En | MEDLINE | ID: mdl-31376938

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator de Crescimento de Hepatócito / Técnicas de Transferência de Genes / Dependovirus / Músculo Esquelético / Superóxido Dismutase-1 / Junção Neuromuscular Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Animals Idioma: En Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator de Crescimento de Hepatócito / Técnicas de Transferência de Genes / Dependovirus / Músculo Esquelético / Superóxido Dismutase-1 / Junção Neuromuscular Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Animals Idioma: En Ano de publicação: 2019 Tipo de documento: Article