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Combination therapy with nusinersen and AVXS-101 in SMA type 1.
Lee, Bo Hoon; Collins, Erin; Lewis, Leann; Guntrum, Debra; Eichinger, Katy; Voter, Karen; Abdel-Hamid, Hoda Z; Ciafaloni, Emma.
Afiliação
  • Lee BH; From Pediatric Neurology (B.H.L.), Department of Neurology (E.C., L.L., D.G., K.E., E.C.), and Department of Pediatric Pulmonology (K.V.), University of Rochester, NY; and Pediatric Neurology (H.Z.A.-H.), Children's Hospital of Pittsburgh of UPMC, PA.
  • Collins E; From Pediatric Neurology (B.H.L.), Department of Neurology (E.C., L.L., D.G., K.E., E.C.), and Department of Pediatric Pulmonology (K.V.), University of Rochester, NY; and Pediatric Neurology (H.Z.A.-H.), Children's Hospital of Pittsburgh of UPMC, PA.
  • Lewis L; From Pediatric Neurology (B.H.L.), Department of Neurology (E.C., L.L., D.G., K.E., E.C.), and Department of Pediatric Pulmonology (K.V.), University of Rochester, NY; and Pediatric Neurology (H.Z.A.-H.), Children's Hospital of Pittsburgh of UPMC, PA.
  • Guntrum D; From Pediatric Neurology (B.H.L.), Department of Neurology (E.C., L.L., D.G., K.E., E.C.), and Department of Pediatric Pulmonology (K.V.), University of Rochester, NY; and Pediatric Neurology (H.Z.A.-H.), Children's Hospital of Pittsburgh of UPMC, PA.
  • Eichinger K; From Pediatric Neurology (B.H.L.), Department of Neurology (E.C., L.L., D.G., K.E., E.C.), and Department of Pediatric Pulmonology (K.V.), University of Rochester, NY; and Pediatric Neurology (H.Z.A.-H.), Children's Hospital of Pittsburgh of UPMC, PA.
  • Voter K; From Pediatric Neurology (B.H.L.), Department of Neurology (E.C., L.L., D.G., K.E., E.C.), and Department of Pediatric Pulmonology (K.V.), University of Rochester, NY; and Pediatric Neurology (H.Z.A.-H.), Children's Hospital of Pittsburgh of UPMC, PA.
  • Abdel-Hamid HZ; From Pediatric Neurology (B.H.L.), Department of Neurology (E.C., L.L., D.G., K.E., E.C.), and Department of Pediatric Pulmonology (K.V.), University of Rochester, NY; and Pediatric Neurology (H.Z.A.-H.), Children's Hospital of Pittsburgh of UPMC, PA.
  • Ciafaloni E; From Pediatric Neurology (B.H.L.), Department of Neurology (E.C., L.L., D.G., K.E., E.C.), and Department of Pediatric Pulmonology (K.V.), University of Rochester, NY; and Pediatric Neurology (H.Z.A.-H.), Children's Hospital of Pittsburgh of UPMC, PA. emma_ciafaloni@urmc.rochester.edu.
Neurology ; 93(14): 640-641, 2019 10 01.
Article em En | MEDLINE | ID: mdl-31488615

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Terapia Genética / Atrofias Musculares Espinais da Infância Tipo de estudo: Diagnostic_studies / Observational_studies Limite: Humans / Infant / Male Idioma: En Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Terapia Genética / Atrofias Musculares Espinais da Infância Tipo de estudo: Diagnostic_studies / Observational_studies Limite: Humans / Infant / Male Idioma: En Ano de publicação: 2019 Tipo de documento: Article