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Neurochemical abnormalities in patients with type 1 Gaucher disease on standard of care therapy.
Kartha, Reena V; Joers, James; Terluk, Marcia R; Travis, Abigail; Rudser, Kyle; Tuite, Paul J; Weinreb, Neal J; Jarnes, Jeanine R; Cloyd, James C; Öz, Gülin.
Afiliação
  • Kartha RV; Center for Orphan Drug Research, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota.
  • Joers J; Department of Experimental and Clinical Pharmacology, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota.
  • Terluk MR; Center for Magnetic Resonance Research, Department of Radiology, University of Minnesota, Minneapolis, Minnesota.
  • Travis A; Center for Orphan Drug Research, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota.
  • Rudser K; Department of Experimental and Clinical Pharmacology, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota.
  • Tuite PJ; Center for Orphan Drug Research, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota.
  • Weinreb NJ; Department of Experimental and Clinical Pharmacology, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota.
  • Jarnes JR; Division of Biostatistics, University of Minnesota, Minneapolis, Minnesota.
  • Cloyd JC; Department of Neurology, University of Minnesota, Minneapolis, Minnesota.
  • Öz G; Department of Human Genetics and Medicine (Hematology), Leonard Miller School of Medicine of University of Miami, Miami, Florida.
J Inherit Metab Dis ; 43(3): 564-573, 2020 05.
Article em En | MEDLINE | ID: mdl-31613991

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Encéfalo / Doença de Gaucher Limite: Adult / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Encéfalo / Doença de Gaucher Limite: Adult / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2020 Tipo de documento: Article