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Cerebrospinal fluid proteomic profiling in nusinersen-treated patients with spinal muscular atrophy.
Kessler, Tobias; Latzer, Pauline; Schmid, Dominic; Warnken, Uwe; Saffari, Afshin; Ziegler, Andreas; Kollmer, Jennifer; Möhlenbruch, Markus; Ulfert, Christian; Herweh, Christian; Wildemann, Brigitte; Wick, Wolfgang; Weiler, Markus.
Afiliação
  • Kessler T; Department of Neurology, Heidelberg University Hospital, Heidelberg, Germany.
  • Latzer P; Clinical Cooperation Unit Neurooncology, German Cancer Consortium (DKTK), German Cancer Research Center (DKFZ), Heidelberg, Germany.
  • Schmid D; Clinical Cooperation Unit Neurooncology, German Cancer Consortium (DKTK), German Cancer Research Center (DKFZ), Heidelberg, Germany.
  • Warnken U; Clinical Cooperation Unit Neurooncology, German Cancer Consortium (DKTK), German Cancer Research Center (DKFZ), Heidelberg, Germany.
  • Saffari A; Medical Faculty, University of Heidelberg, Heidelberg, Germany.
  • Ziegler A; Functional Proteomic Analysis, German Cancer Research Center (DKFZ), Heidelberg, Germany.
  • Kollmer J; Division of Child Neurology and Metabolic Medicine, Center for Child and Adolescent Medicine, Heidelberg University Hospital, Heidelberg, Germany.
  • Möhlenbruch M; Division of Child Neurology and Metabolic Medicine, Center for Child and Adolescent Medicine, Heidelberg University Hospital, Heidelberg, Germany.
  • Ulfert C; Department of Neuroradiology, Heidelberg University Hospital, Heidelberg, Germany.
  • Herweh C; Department of Neuroradiology, Heidelberg University Hospital, Heidelberg, Germany.
  • Wildemann B; Department of Neuroradiology, Heidelberg University Hospital, Heidelberg, Germany.
  • Wick W; Department of Neuroradiology, Heidelberg University Hospital, Heidelberg, Germany.
  • Weiler M; Department of Neurology, Heidelberg University Hospital, Heidelberg, Germany.
J Neurochem ; 153(5): 650-661, 2020 06.
Article em En | MEDLINE | ID: mdl-31903607

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Atrofia Muscular Espinal / Proteômica Tipo de estudo: Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Atrofia Muscular Espinal / Proteômica Tipo de estudo: Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2020 Tipo de documento: Article