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Janus Kinase Inhibition in the Aicardi-Goutières Syndrome.
Vanderver, Adeline; Adang, Laura; Gavazzi, Francesco; McDonald, Katherine; Helman, Guy; Frank, David B; Jaffe, Nicole; Yum, Sabrina W; Collins, Abigail; Keller, Stephanie R; Lebon, Pierre; Meritet, Jean-François; Rhee, Jullie; Takanohashi, Asako; Armangue, Thais; Ulrick, Nicole; Sherbini, Omar; Koh, Jamie; Peer, Kyle; Besnier, Constance; Scher, Carly; Boyle, Katherine; Dubbs, Holly; Kramer-Golinkoff, Julia; Pizzino, Amy; Woidill, Sarah; Shults, Justine.
Afiliação
  • Vanderver A; Children's Hospital of Philadelphia, Philadelphia, PA vandervera@email.chop.edu.
  • Adang L; Children's Hospital of Philadelphia, Philadelphia, PA vandervera@email.chop.edu.
  • Gavazzi F; Children's Hospital of Philadelphia, Philadelphia, PA vandervera@email.chop.edu.
  • McDonald K; Children's Hospital of Philadelphia, Philadelphia, PA vandervera@email.chop.edu.
  • Helman G; Royal Children's Hospital Melbourne, Melbourne, VIC, Australia.
  • Frank DB; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Jaffe N; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Yum SW; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Collins A; Children's Hospital Colorado, Aurora, CO.
  • Keller SR; Children's Healthcare of Atlanta, Atlanta, GA.
  • Lebon P; Faculté de Médecine Université Paris Descartes, Paris, France.
  • Meritet JF; Hôpital Cochin, Paris, France.
  • Rhee J; Children's National Health System, Washington, DC.
  • Takanohashi A; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Armangue T; Sant Joan de Déu Children's Hospital, Barcelona, Spain.
  • Ulrick N; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Sherbini O; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Koh J; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Peer K; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Besnier C; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Scher C; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Boyle K; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Dubbs H; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Kramer-Golinkoff J; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Pizzino A; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Woidill S; Children's Hospital of Philadelphia, Philadelphia, PA.
  • Shults J; University of Pennsylvania, Philadelphia, PA.
N Engl J Med ; 383(10): 986-989, 2020 09 03.
Article em En | MEDLINE | ID: mdl-32877590

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Sulfonamidas / Azetidinas / Doenças Autoimunes do Sistema Nervoso / Inibidores de Janus Quinases / Malformações do Sistema Nervoso Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Sulfonamidas / Azetidinas / Doenças Autoimunes do Sistema Nervoso / Inibidores de Janus Quinases / Malformações do Sistema Nervoso Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male Idioma: En Ano de publicação: 2020 Tipo de documento: Article