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Danicopan: an oral complement factor D inhibitor for paroxysmal nocturnal hemoglobinuria
Risitano, Antonio M; Kulasekararaj, Austin G; Lee, Jong Wook; Maciejewski, Jaroslaw P; Notaro, Rosario; Brodsky, Robert; Huang, Mingjun; Geffner, Michael; Browett, Peter.
Afiliação
  • Risitano AM; Federico II University of Naples, Naples, Italy and AORN Moscati, Avellino. amrisita@unina.it.
  • Kulasekararaj AG; King's College Hospital-NHS Foundation Trust, NIHR/Wellcome King's Clinical Research Facility, London, UK and King's College London, London.
  • Lee JW; Seoul St. Mary's Hospital, The Catholic University of Korea, Seoul.
  • Maciejewski JP; Cleveland Clinic, Cleveland, OH.
  • Notaro R; Core Research Laboratory, Istituto per lo Studio, la Prevenzione e la Rete Oncologica (ISPRO), Firenze, Italy; Azienda Ospedaliera-Universitaria Careggi, Firenze.
  • Brodsky R; Johns Hopkins University School of Medicine, Baltimore, MD.
  • Huang M; Achillion, Inc., A Subsidiary of Alexion Pharmaceuticals, Inc., New Haven, CT, USA; Alexion Pharmaceuticals, New Haven CT.
  • Geffner M; Achillion Inc., A Subsidiary of Alexion Pharmaceuticals, Inc., Blue Bell, PA.
  • Browett P; University of Auckland, Auckland.
Haematologica ; 106(12): 3188-3197, 2021 12 01.
Article em En | MEDLINE | ID: mdl-33121236

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator D do Complemento / Hemoglobinúria Paroxística Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator D do Complemento / Hemoglobinúria Paroxística Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article