Metachromatic Leukodystrophy: Diagnosis, Modeling, and Treatment Approaches.

Shaimardanova, Alisa A; Chulpanova, Daria S; Solovyeva, Valeriya V; Mullagulova, Aysilu I; Kitaeva, Kristina V; Allegrucci, Cinzia; Rizvanov, Albert A

Shaimardanova, Alisa A; Chulpanova, Daria S; Solovyeva, Valeriya V; Mullagulova, Aysilu I; Kitaeva, Kristina V; Allegrucci, Cinzia; Rizvanov, Albert A.

Afiliação

Shaimardanova AA; Institute of Fundamental Medicine and Biology, Kazan Federal University, Kazan, Russia.
Chulpanova DS; Institute of Fundamental Medicine and Biology, Kazan Federal University, Kazan, Russia.
Solovyeva VV; Shemyakin-Ovchinnikov Institute of Bioorganic Chemistry, The Russian Academy of Sciences, Moscow, Russia.
Mullagulova AI; Institute of Fundamental Medicine and Biology, Kazan Federal University, Kazan, Russia.
Kitaeva KV; Shemyakin-Ovchinnikov Institute of Bioorganic Chemistry, The Russian Academy of Sciences, Moscow, Russia.
Allegrucci C; Institute of Fundamental Medicine and Biology, Kazan Federal University, Kazan, Russia.
Rizvanov AA; Institute of Fundamental Medicine and Biology, Kazan Federal University, Kazan, Russia.

Front Med (Lausanne) ; 7: 576221, 2020.

Article em En | MEDLINE | ID: mdl-33195324

Palavras-chave

arylsulfatase A; bone marrow transplantation; gene therapy; lysosomal storage diseases; mesenchymal stem cells; metachromatic leukodystrophy; replacement therapy; sulfatide

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Texto completo: 1 Base de dados: MEDLINE Tipo de estudo: Diagnostic_studies Idioma: En Ano de publicação: 2020 Tipo de documento: Article

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Texto completo: 1 Base de dados: MEDLINE Tipo de estudo: Diagnostic_studies Idioma: En Ano de publicação: 2020 Tipo de documento: Article