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One-year outcomes from a phase 3 randomized trial of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria who received prior eculizumab.
Kulasekararaj, Austin G; Hill, Anita; Langemeijer, Saskia; Wells, Richard; González Fernández, F Ataúlfo; Gaya, Anna; Ojeda Gutierrez, Emilio; Piatek, Caroline I; Mitchell, Lindsay; Usuki, Kensuke; Bosi, Alberto; Brodsky, Robert A; Ogawa, Masayo; Yu, Ji; Ortiz, Stephan; Röth, Alexander; Lee, Jong Wook; Peffault de Latour, Régis.
Afiliação
  • Kulasekararaj AG; Department of Haematological Medicine, King's College Hospital, National Institute of Health Research/Wellcome King's Clinical Research Facility and King's College London, London, UK.
  • Hill A; Department of Haematology, Leeds Teaching Hospitals, Leeds, UK.
  • Langemeijer S; Radboudumc, Nijmegen, the Netherlands.
  • Wells R; Sunnybrook Health Sciences Centre, Toronto, ON, Canada.
  • González Fernández FA; Department of Hematology, Hospital Clinico Universitario San Carlos, The Clinic Institute of Haematological and Oncological Diseases, Madrid, Spain.
  • Gaya A; Department of Hematology, Hospital Clinic de Barcelona, Barcelona, Spain.
  • Ojeda Gutierrez E; Hospital Universitario Puerta de Hierro Majadahonda, Madrid, Spain.
  • Piatek CI; Jane Anne Nohl Division of Hematology, Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • Mitchell L; Monklands Hospital, Airdrie, Scotland, UK.
  • Usuki K; NTT Medical Center Tokyo, Tokyo, Japan.
  • Bosi A; Department of Experimental and Clinical Medicine, University of Florence, Florence, Italy.
  • Brodsky RA; The John Hopkins University School of Medicine, Baltimore, MD, USA.
  • Ogawa M; Alexion Pharmaceuticals, Inc., Boston, MA, USA.
  • Yu J; Alexion Pharmaceuticals, Inc., Boston, MA, USA.
  • Ortiz S; Alexion Pharmaceuticals, Inc., Boston, MA, USA.
  • Röth A; Department of Hematology, West German Cancer Center, University Hospital Essen, Essen, Germany.
  • Lee JW; Department of Hematology, Seoul St. Mary's Hospital, The Catholic University of Korea, Seoul, Republic of Korea.
  • Peffault de Latour R; Bone Marrow Transplantation Unit, Saint Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.
Eur J Haematol ; 106(3): 389-397, 2021 Mar.
Article em En | MEDLINE | ID: mdl-33301613

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Inativadores do Complemento / Anticorpos Monoclonais Humanizados / Hemoglobinúria Paroxística Tipo de estudo: Clinical_trials / Diagnostic_studies Limite: Adult / Female / Humans / Male Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Inativadores do Complemento / Anticorpos Monoclonais Humanizados / Hemoglobinúria Paroxística Tipo de estudo: Clinical_trials / Diagnostic_studies Limite: Adult / Female / Humans / Male Idioma: En Ano de publicação: 2021 Tipo de documento: Article