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Gain of toxic function by long-term AAV9-mediated SMN overexpression in the sensorimotor circuit.
Van Alstyne, Meaghan; Tattoli, Ivan; Delestrée, Nicolas; Recinos, Yocelyn; Workman, Eileen; Shihabuddin, Lamya S; Zhang, Chaolin; Mentis, George Z; Pellizzoni, Livio.
Afiliação
  • Van Alstyne M; Center for Motor Neuron Biology and Disease, Columbia University, New York, NY, USA.
  • Tattoli I; Department of Pathology and Cell Biology, Columbia University, New York, NY, USA.
  • Delestrée N; Department of Neurology, Columbia University, New York, NY, USA.
  • Recinos Y; Center for Motor Neuron Biology and Disease, Columbia University, New York, NY, USA.
  • Workman E; Department of Pathology and Cell Biology, Columbia University, New York, NY, USA.
  • Shihabuddin LS; Center for Motor Neuron Biology and Disease, Columbia University, New York, NY, USA.
  • Zhang C; Department of Pathology and Cell Biology, Columbia University, New York, NY, USA.
  • Mentis GZ; Department of Neurology, Columbia University, New York, NY, USA.
  • Pellizzoni L; Center for Motor Neuron Biology and Disease, Columbia University, New York, NY, USA.
Nat Neurosci ; 24(7): 930-940, 2021 07.
Article em En | MEDLINE | ID: mdl-33795885

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Proteína 1 de Sobrevivência do Neurônio Motor / Neurônios Motores / Degeneração Neural Limite: Animals Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Proteína 1 de Sobrevivência do Neurônio Motor / Neurônios Motores / Degeneração Neural Limite: Animals Idioma: En Ano de publicação: 2021 Tipo de documento: Article