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Investigation of ALPL variant states and clinical outcomes: An analysis of adults and adolescents with hypophosphatasia treated with asfotase alfa.
Kishnani, Priya S; Del Angel, Guillermo; Zhou, Shanggen; Rush, Eric T.
Afiliação
  • Kishnani PS; Department of Pediatrics, Duke University Medical Center, 2351 Erwin Road, Durham, NC, USA. Electronic address: Priya.Kishnani@duke.edu.
  • Del Angel G; Alexion Pharmaceuticals, Inc., 121 Seaport Blvd., Boston, MA, USA. Electronic address: Guillermo.delAngel@alexion.com.
  • Zhou S; Covance, Inc., 206 Carnegie Center Dr, Princeton, NJ, USA. Electronic address: shanggen.zhou@covance.com.
  • Rush ET; Children's Mercy Hospital Kansas City, 2401 Gillham Rd, Kansas City, MO, USA; University of Missouri-Kansas City School of Medicine, Kansas City, MO, USA; University of Kansas School of Medicine, Kansas City, KS, USA. Electronic address: etrush@cmh.edu.
Mol Genet Metab ; 133(1): 113-121, 2021 05.
Article em En | MEDLINE | ID: mdl-33814268

Texto completo: 1 Eixos temáticos: Pesquisa_clinica Base de dados: MEDLINE Assunto principal: Proteínas Recombinantes de Fusão / Imunoglobulina G / Fosfatase Alcalina / Hipofosfatasia Tipo de estudo: Clinical_trials / Prognostic_studies Limite: Adolescent / Adult / Female / Humans / Male Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Eixos temáticos: Pesquisa_clinica Base de dados: MEDLINE Assunto principal: Proteínas Recombinantes de Fusão / Imunoglobulina G / Fosfatase Alcalina / Hipofosfatasia Tipo de estudo: Clinical_trials / Prognostic_studies Limite: Adolescent / Adult / Female / Humans / Male Idioma: En Ano de publicação: 2021 Tipo de documento: Article