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Trametinib therapy for children with neurofibromatosis type 1 and life-threatening plexiform neurofibroma or treatment-refractory low-grade glioma.
Ronsley, Rebecca; Hounjet, Celine D; Cheng, Sylvia; Rassekh, Shahrad Rod; Duncan, Walter J; Dunham, Christopher; Gardiner, Jane; Ghag, Arvindera; Ludemann, Jeffrey P; Wensley, David; Rehmus, Wingfield; Sargent, Michael A; Hukin, Juliette.
Afiliação
  • Ronsley R; Division of Hematology, Oncology & BMT, Department of Pediatrics, University of British Columbia, Vancouver, Canada.
  • Hounjet CD; Faculty of Medicine, University of British Columbia, Vancouver, Canada.
  • Cheng S; Division of Hematology, Oncology & BMT, Department of Pediatrics, University of British Columbia, Vancouver, Canada.
  • Rassekh SR; Division of Hematology, Oncology & BMT, Department of Pediatrics, University of British Columbia, Vancouver, Canada.
  • Duncan WJ; Division of Pediatric Cardiology, Department of Pediatrics, University of British Columbia, Vancouver, Canada.
  • Dunham C; Division of Anatomic Pathology, Department of Pathology, University of British Columbia, Vancouver, Canada.
  • Gardiner J; Division of Pediatric Ophthalmology, Department of Surgery, University of British Columbia, Vancouver, Canada.
  • Ghag A; Division of Pediatric Orthopedic Surgery, Department of Surgery, University of British Columbia, Vancouver, Canada.
  • Ludemann JP; Division of Pediatric Otolaryngology, Department of Surgery, University of British Columbia, Vancouver, Canada.
  • Wensley D; Division of Pediatric Respiratory Medicine, Department of Pediatrics, University of British Columbia, Vancouver, Canada.
  • Rehmus W; Division of Dermatology, Department of Pediatrics, University of British Columbia, Vancouver, Canada.
  • Sargent MA; Division of Pediatric Neuro-Radiology, Department of Radiology, University of British Columbia, Vancouver, Canada.
  • Hukin J; Division of Hematology, Oncology & BMT, Department of Pediatrics, University of British Columbia, Vancouver, Canada.
Cancer Med ; 10(11): 3556-3564, 2021 06.
Article em En | MEDLINE | ID: mdl-33939292

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Piridonas / Pirimidinonas / Neoplasias Encefálicas / Neurofibromatose 1 / Neurofibroma Plexiforme / Glioma / Antineoplásicos Tipo de estudo: Observational_studies Limite: Adolescent / Child / Child, preschool / Female / Humans / Infant / Male País como assunto: America do norte Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Piridonas / Pirimidinonas / Neoplasias Encefálicas / Neurofibromatose 1 / Neurofibroma Plexiforme / Glioma / Antineoplásicos Tipo de estudo: Observational_studies Limite: Adolescent / Child / Child, preschool / Female / Humans / Infant / Male País como assunto: America do norte Idioma: En Ano de publicação: 2021 Tipo de documento: Article