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Production of therapeutic iduronate-2-sulfatase enzyme with a novel single-stranded RNA virus vector.
Ohira, Mari; Kikuchi, Emika; Mizuta, Shiori; Yoshida, Naomi; Onodera, Masafumi; Nakanishi, Mahito; Okuyama, Torayuki; Mashima, Ryuichi.
Afiliação
  • Ohira M; Department of Clinical Laboratory Medicine, National Center for Child Health and Development, Tokyo, Japan.
  • Kikuchi E; Department of Clinical Laboratory Medicine, National Center for Child Health and Development, Tokyo, Japan.
  • Mizuta S; TOKIWA-Bio Inc, Tsukuba-city, Japan.
  • Yoshida N; TOKIWA-Bio Inc, Tsukuba-city, Japan.
  • Onodera M; Department of Human Genetics, National Research Institute for Child Health and Development, Tokyo, Japan.
  • Nakanishi M; TOKIWA-Bio Inc, Tsukuba-city, Japan.
  • Okuyama T; Department of Clinical Laboratory Medicine, National Center for Child Health and Development, Tokyo, Japan.
  • Mashima R; Department of Clinical Laboratory Medicine, National Center for Child Health and Development, Tokyo, Japan.
Genes Cells ; 26(11): 891-904, 2021 Nov.
Article em En | MEDLINE | ID: mdl-34480399

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Vírus de RNA / Mucopolissacaridose II / Iduronato Sulfatase Limite: Animals / Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Vírus de RNA / Mucopolissacaridose II / Iduronato Sulfatase Limite: Animals / Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article