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Rational engineering of a functional CpG-free ITR for AAV gene therapy.
Pan, Xiufang; Yue, Yongping; Boftsi, Maria; Wasala, Lakmini P; Tran, Ngoc Tam; Zhang, Keqing; Pintel, David J; Tai, Phillip W L; Duan, Dongsheng.
Afiliação
  • Pan X; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO, 65212, USA.
  • Yue Y; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO, 65212, USA.
  • Boftsi M; Pathobiology Area Graduate Program, University of Missouri, Columbia, MO, 65212, USA.
  • Wasala LP; Christopher S. Bond Life Sciences Center, University of Missouri, Columbia, MO, 65212, USA.
  • Tran NT; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO, 65212, USA.
  • Zhang K; Pathobiology Area Graduate Program, University of Missouri, Columbia, MO, 65212, USA.
  • Pintel DJ; Horae Gene Therapy Center, UMass Chan Medical School, Worcester, MA, 01605, USA.
  • Tai PWL; Department of Microbiology and Physiological Systems, UMass Chan Medical School, Worcester, MA, 01605, USA.
  • Duan D; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO, 65212, USA.
Gene Ther ; 29(6): 333-345, 2022 06.
Article em En | MEDLINE | ID: mdl-34611321

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Dependovirus / Vetores Genéticos Limite: Animals Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Dependovirus / Vetores Genéticos Limite: Animals Idioma: En Ano de publicação: 2022 Tipo de documento: Article