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Splice correction therapies for familial hypercholesterolemic patients with low-density lipoprotein receptor mutations.
McIntosh, Craig S; Watts, Gerald F; Wilton, Steve D; Aung-Htut, May T.
Afiliação
  • McIntosh CS; Perron Institute for Neurological and Translational Science, Nedlands, Western Australia, Australia.
  • Watts GF; Centre for Molecular Medicine and Innovative Therapeutics, Health Futures Institute, Murdoch University, Murdoch, Western Australia, Australia.
  • Wilton SD; School of Medicine, University of Western Australia.
  • Aung-Htut MT; Lipid Disorders Clinic, Department of Cardiology, Royal Perth Hospital, Perth, Western Australia, Australia.
Curr Opin Lipidol ; 32(6): 355-362, 2021 12 01.
Article em En | MEDLINE | ID: mdl-34653074

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Receptores de LDL / Hiperlipoproteinemia Tipo II Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Receptores de LDL / Hiperlipoproteinemia Tipo II Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article