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Preclinical pharmacology of glucosylceramide synthase inhibitor venglustat in a GBA-related synucleinopathy model.
Viel, Catherine; Clarke, Jennifer; Kayatekin, Can; Richards, Amy M; Chiang, Ming Sum R; Park, Hyejung; Wang, Bing; Shihabuddin, Lamya S; Sardi, S Pablo.
Afiliação
  • Viel C; Rare and Neurologic Diseases, Sanofi, 49 New York Avenue, Framingham, MA, 01701, USA.
  • Clarke J; Rare and Neurologic Diseases, Sanofi, 49 New York Avenue, Framingham, MA, 01701, USA.
  • Kayatekin C; Rare and Neurologic Diseases, Sanofi, 49 New York Avenue, Framingham, MA, 01701, USA.
  • Richards AM; Genomic Medicine Unit, Sanofi, Framingham, MA, 01701, USA.
  • Chiang MSR; Rare and Neurologic Diseases, Sanofi, 49 New York Avenue, Framingham, MA, 01701, USA.
  • Park H; US Early Development for Synthetics Platform, Sanofi, Waltham, MA, 02451, USA.
  • Wang B; US Early Development for Synthetics Platform, Sanofi, Waltham, MA, 02451, USA.
  • Shihabuddin LS; Rare and Neurologic Diseases, Sanofi, 49 New York Avenue, Framingham, MA, 01701, USA.
  • Sardi SP; 5AM Ventures, Boston, MA, 02116, USA.
Sci Rep ; 11(1): 20945, 2021 10 22.
Article em En | MEDLINE | ID: mdl-34686711

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Quinuclidinas / Carbamatos / Sinucleinopatias / Glucosilceramidase / Glucosilceramidas / Glucosiltransferases Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Animals Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Quinuclidinas / Carbamatos / Sinucleinopatias / Glucosilceramidase / Glucosilceramidas / Glucosiltransferases Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Animals Idioma: En Ano de publicação: 2021 Tipo de documento: Article