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Meta-analyses of deflazacort versus prednisone/prednisolone in patients with nonsense mutation Duchenne muscular dystrophy.
Shieh, Perry B; Elfring, Gary; Trifillis, Panayiota; Santos, Claudio; Peltz, Stuart W; Parsons, Julie A; Apkon, Susan; Darras, Basil T; Campbell, Craig; McDonald, Craig M.
Afiliação
  • Shieh PB; University of California at Los Angeles, Los Angeles, CA, USA.
  • Elfring G; PTC Therapeutics, Inc., South Plainfield, NJ, USA.
  • Trifillis P; PTC Therapeutics, Inc., South Plainfield, NJ, USA.
  • Santos C; PTC Therapeutics, Inc., South Plainfield, NJ, USA.
  • Peltz SW; PTC Therapeutics, Inc., South Plainfield, NJ, USA.
  • Parsons JA; University of Colorado School of Medicine, Aurora, CO, USA.
  • Apkon S; University of Colorado School of Medicine, Aurora, CO, USA.
  • Darras BT; Boston Children's Hospital, Boston, MA, USA.
  • Campbell C; Children's Hospital - London Health Sciences Centre, University of Western Ontario, London, ON, Canada.
  • McDonald CM; University of California Davis Health, Sacramento, CA, USA.
J Comp Eff Res ; 10(18): 1337-1347, 2021 12.
Article em En | MEDLINE | ID: mdl-34693725

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Códon sem Sentido / Distrofia Muscular de Duchenne Tipo de estudo: Observational_studies / Systematic_reviews Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Códon sem Sentido / Distrofia Muscular de Duchenne Tipo de estudo: Observational_studies / Systematic_reviews Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article