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[Pharmacological property, mechanism of action and clinical study results of Pabinafusp Alfa (Genetical Recombination) (IZCARGO® I.V. Infusion 10 mg) as the therapeutic for Mucopolysaccharidosis type-II (Hunter syndrome)].
Yamamoto, Ryuji; Kawashima, Satoshi.
Afiliação
  • Yamamoto R; Pharmacology & Toxicology Unit, Drug Discovery Research Institute, Research Division, JCR Pharmaceuticals Co., Ltd.
  • Kawashima S; Planning Department, Development Division, JCR Pharmaceuticals Co., Ltd.
Nihon Yakurigaku Zasshi ; 157(1): 62-75, 2022.
Article em Ja | MEDLINE | ID: mdl-34980815

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Mucopolissacaridose II / Iduronato Sulfatase Tipo de estudo: Prognostic_studies Limite: Animals / Humans Idioma: Ja Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Mucopolissacaridose II / Iduronato Sulfatase Tipo de estudo: Prognostic_studies Limite: Animals / Humans Idioma: Ja Ano de publicação: 2022 Tipo de documento: Article